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Effectiveness and safety of everolimus treatment in patients with tuberous sclerosis complex in real-world clinical practice.
Cockerell, Ine; Christensen, Jakob; Hoei-Hansen, Christina E; Holst, Lotte; Grenaa Frederiksen, Mikkel; Issa-Epe, Aart Imran; Nedregaard, Bård; Solhoff, Ragnar; Heimdal, Ketil; Johannessen Landmark, Cecilie; Lund, Caroline; Nærland, Terje.
Afiliación
  • Cockerell I; Department of Rare Disorders and Disabilities, National Centre for Rare Epilepsy-Related Disorders, Oslo University Hospital, Pb 4950, 0424, Nydalen, Oslo, Norway. inec@ous-hf.no.
  • Christensen J; Department of Clinical Medicine, Aarhus University, Aarhus, Denmark.
  • Hoei-Hansen CE; Department of Neurology, Aarhus University Hospital, Affiliated Member of the European Reference Network EpiCARE, Aarhus, Denmark.
  • Holst L; Department of Clinical Medicine, Copenhagen University, Copenhagen, Denmark.
  • Grenaa Frederiksen M; Department of Paediatrics, University Hospital Rigshospitalet, Copenhagen, Denmark.
  • Issa-Epe AI; Department of Clinical Medicine, Aarhus University, Aarhus, Denmark.
  • Nedregaard B; Department of Paediatrics, University Hospital Rigshospitalet, Copenhagen, Denmark.
  • Solhoff R; Section of Abdominal Radiology, Department of Radiology, Oslo University Hospital, Oslo, Norway.
  • Heimdal K; Section of Neuroradiology, Department of Radiology, Oslo University Hospital, Oslo, Norway.
  • Johannessen Landmark C; Department of Neurology, Sørlandet Hospital, Arendal, Norway.
  • Lund C; Department of Medical Genetics, Oslo University Hospital, Oslo, Norway.
  • Nærland T; Department of Pharmacy, Faculty of Health Sciences, Oslo Metropolitan University, Oslo, Norway.
Orphanet J Rare Dis ; 18(1): 377, 2023 Dec 02.
Article en En | MEDLINE | ID: mdl-38042867

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Astrocitoma / Esclerosis Tuberosa / Angiomiolipoma / Epilepsia / Neoplasias Renales / Antineoplásicos Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2023 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Astrocitoma / Esclerosis Tuberosa / Angiomiolipoma / Epilepsia / Neoplasias Renales / Antineoplásicos Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2023 Tipo del documento: Article