Detalhe da pesquisa
1.
Topical cystic fibrosis transmembrane conductance regulator gene replacement for cystic fibrosis-related lung disease.
Cochrane Database Syst Rev;
(6): CD005599, 2016 Jun 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-27314455
2.
Treatment of autosomal dominant hearing loss by in vivo delivery of genome editing agents.
Nature;
553(7687): 217-221, 2018 01 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-29258297
3.
Therapeutic genome editing of triple-negative breast tumors using a noncationic and deformable nanolipogel.
Proc Natl Acad Sci U S A;
116(37): 18295-18303, 2019 09 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-31451668
4.
Genetic approaches to the treatment of inherited neuromuscular diseases.
Hum Mol Genet;
28(R1): R55-R64, 2019 10 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-31227836
5.
Intrathecal gene therapy in mouse models expressing CMT1X mutations.
Hum Mol Genet;
27(8): 1460-1473, 2018 04 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-29462293
6.
Dual-Modified Liposome for Targeted and Enhanced Gene Delivery into Mice Brain.
J Pharmacol Exp Ther;
374(3): 354-365, 2020 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32561686
7.
Effective naked plasmid DNA delivery into stem cells by microextrusion-based transient-transfection system for in situ cardiac repair.
Cytotherapy;
22(2): 70-81, 2020 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-32007417
8.
Gene replacement therapy in a model of Charcot-Marie-Tooth 4C neuropathy.
Brain;
142(5): 1227-1241, 2019 05 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-30907403
9.
Delivering the Messenger: Advances in Technologies for Therapeutic mRNA Delivery.
Mol Ther;
27(4): 710-728, 2019 04 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30846391
10.
Enhancement of sciatic nerve regeneration with dual delivery of vascular endothelial growth factor and nerve growth factor genes.
J Nanobiotechnology;
18(1): 46, 2020 Mar 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-32169062
11.
Lipoplex-based targeted gene therapy for the suppression of tumours with VEGFR expression by producing anti-angiogenic molecules.
J Nanobiotechnology;
18(1): 58, 2020 Apr 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32272948
12.
Bioreducible crosslinked cationic nanopolyplexes from clickable polyethylenimines enabling robust cancer gene therapy.
Nanomedicine;
24: 102144, 2020 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-31838150
13.
Dual-targeted NIS polyplexes-a theranostic strategy toward tumors with heterogeneous receptor expression.
Gene Ther;
26(3-4): 93-108, 2019 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-30683895
14.
Combination of cytokine-enhanced vaccine and chemo-gene therapy as surgery adjuvant treatments for spontaneous canine melanoma.
Gene Ther;
26(10-11): 418-431, 2019 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-30858538
15.
Efficient penetration of Scp01-b and its DNA transfer abilities into cells.
J Cell Physiol;
234(5): 6539-6547, 2019 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-30230543
16.
Golgi-retained Cx32 mutants interfere with gene addition therapy for CMT1X.
Hum Mol Genet;
26(9): 1622-1633, 2017 05 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-28334782
17.
Current and innovative emerging therapies for porphyrias with hepatic involvement.
J Hepatol;
71(2): 422-433, 2019 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-31102718
18.
Application of biomaterials to advance induced pluripotent stem cell research and therapy.
EMBO J;
34(8): 987-1008, 2015 Apr 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-25766254
19.
Cationic micelle: A promising nanocarrier for gene delivery with high transfection efficiency.
J Gene Med;
21(7): e3101, 2019 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-31170324
20.
Naked pDNA Inhalation Powder Composed of Hyaluronic Acid Exhibits High Gene Expression in the Lungs.
Mol Pharm;
16(2): 489-497, 2019 02 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-30092131