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Once-weekly prophylaxis with glycoPEGylated recombinant factor VIII (N8-GP) in severe haemophilia A: Safety and efficacy results from pathfinder 2 (randomized phase III trial).
Curry, Nicola; Albayrak, Canan; Escobar, Miguel; Andre Holme, Pål; Kearney, Susan; Klamroth, Robert; Misgav, Mudi; Négrier, Claude; Wheeler, Allison; Santagostino, Elena; Shima, Midori; Landorph, Andrea; Tønder, Sidsel Marie; Lentz, Steven R.
Afiliación
  • Curry N; Oxford Haemophilia and Thrombosis Centre and Oxford NIHR BRC, Churchill Hospital, Oxford, UK.
  • Albayrak C; Department of Pediatric Hematology and Oncology, Faculty of Medicine, Ondokuz Mayis University, Samsun, Turkey.
  • Escobar M; McGovern Medical School and the Gulf States Hemophilia and Thrombophilia Center, University of Texas Health Science Center, Houston, Texas.
  • Andre Holme P; Department of Haematology, Institute of Clinical Medicine, University of Oslo, Oslo University Hospital, Oslo, Norway.
  • Kearney S; CHCMN Hemophilia and Thrombosis Center, Children's Hospital and Clinics of Minnesota, Minneapolis, Minnesota.
  • Klamroth R; Haemophiliezentrum, Klinik für Innere Medizin, Vivantes Klinikum im Friedrichshain, Berlin, Germany.
  • Misgav M; The National Hemophilia Center and Center of Thrombosis, Chaim Sheba Medical Center, Sackler School of Medicine, Tel Aviv University, Tel Aviv, Israel.
  • Négrier C; Hôpital Louis Pradel, Université Claude Bernard, Lyon, France.
  • Wheeler A; Pathology, Microbiology and Immunology, Vanderbilt University School of Medicine, Nashville, Tennessee.
  • Santagostino E; Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, IRCCS Cà Granda Foundation, Maggiore Hospital Policlinic, Milan, Italy.
  • Shima M; Department of Pediatrics, Nara Hemophilia Centre, Nara Medical University, Kashihara, Nara, Japan.
  • Landorph A; Novo Nordisk A/S, Søborg, Denmark.
  • Tønder SM; Novo Nordisk A/S, Søborg, Denmark.
  • Lentz SR; Division of Hematology, Oncology, and Blood and Marrow Transplantation, Department of Internal Medicine, University of Iowa Carver College of Medicine, Iowa City, Iowa.
Haemophilia ; 25(3): 373-381, 2019 May.
Article en En | MEDLINE | ID: mdl-30817066

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Polietilenglicoles / Seguridad / Factor VIII / Hemofilia A Tipo de estudio: Clinical_trials Límite: Adult / Female / Humans / Male Idioma: En Revista: Haemophilia Asunto de la revista: HEMATOLOGIA Año: 2019 Tipo del documento: Article País de afiliación: Reino Unido

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Polietilenglicoles / Seguridad / Factor VIII / Hemofilia A Tipo de estudio: Clinical_trials Límite: Adult / Female / Humans / Male Idioma: En Revista: Haemophilia Asunto de la revista: HEMATOLOGIA Año: 2019 Tipo del documento: Article País de afiliación: Reino Unido