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Clinical development of triple-combination CFTR modulators for cystic fibrosis patients with one or two F508del alleles.
Taylor-Cousar, Jennifer L; Mall, Marcus A; Ramsey, Bonnie W; McKone, Edward F; Tullis, Elizabeth; Marigowda, Gautham; McKee, Charlotte M; Waltz, David; Moskowitz, Samuel M; Savage, Jessica; Xuan, Fengjuan; Rowe, Steven M.
Afiliación
  • Taylor-Cousar JL; National Jewish Health, Denver, CO, USA.
  • Mall MA; Charité - Universitätsmedizin Berlin, Berlin Institute of Health, German Center for Lung Research, Berlin, Germany.
  • Ramsey BW; Seattle Children's Hospital, Seattle, WA, USA.
  • McKone EF; St Vincent's University Hospital and University College Dublin School of Medicine, Dublin, Ireland.
  • Tullis E; St Michael's Hospital, Toronto, ON, Canada.
  • Marigowda G; Vertex Pharmaceuticals Inc., Boston, MA, USA.
  • McKee CM; Vertex Pharmaceuticals Inc., Boston, MA, USA.
  • Waltz D; Vertex Pharmaceuticals Inc., Boston, MA, USA.
  • Moskowitz SM; Vertex Pharmaceuticals Inc., Boston, MA, USA.
  • Savage J; Vertex Pharmaceuticals Inc., Boston, MA, USA.
  • Xuan F; Vertex Pharmaceuticals Inc., Boston, MA, USA.
  • Rowe SM; Gregory Fleming James Cystic Fibrosis Research Center, University of Alabama at Birmingham, Birmingham, AL, USA.
ERJ Open Res ; 5(2)2019 Apr.
Article en En | MEDLINE | ID: mdl-31218221

Texto completo: 1 Banco de datos: MEDLINE Tipo de estudio: Clinical_trials Idioma: En Revista: ERJ Open Res Año: 2019 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Banco de datos: MEDLINE Tipo de estudio: Clinical_trials Idioma: En Revista: ERJ Open Res Año: 2019 Tipo del documento: Article País de afiliación: Estados Unidos