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1.
Control of backbone chemistry and chirality boost oligonucleotide splice switching activity.
Nucleic Acids Res
; 50(10): 5443-5466, 2022 06 10.
Article
in English
| MEDLINE | ID: mdl-35061895
2.
Endogenous ADAR-mediated RNA editing in non-human primates using stereopure chemically modified oligonucleotides.
Nat Biotechnol
; 40(7): 1093-1102, 2022 07.
Article
in English
| MEDLINE | ID: mdl-35256816
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