Search details
1.
IS-Seq: a bioinformatics pipeline for integration sites analysis with comprehensive abundance quantification methods.
BMC Bioinformatics
; 24(1): 286, 2023 Jul 18.
Article
in English
| MEDLINE | ID: mdl-37464281
2.
High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing.
Mol Ther
; 30(10): 3209-3225, 2022 10 05.
Article
in English
| MEDLINE | ID: mdl-35614857
3.
Multiparametric Whole Blood Dissection: A one-shot comprehensive picture of the human hematopoietic system.
Cytometry A
; 91(10): 952-965, 2017 10.
Article
in English
| MEDLINE | ID: mdl-28609016
4.
CRISPR-SURF: discovering regulatory elements by deconvolution of CRISPR tiling screen data.
Nat Methods
; 15(12): 992-993, 2018 12.
Article
in English
| MEDLINE | ID: mdl-30504875
5.
Preclinical safety and efficacy of human CD34(+) cells transduced with lentiviral vector for the treatment of Wiskott-Aldrich syndrome.
Mol Ther
; 21(1): 175-84, 2013 Jan.
Article
in English
| MEDLINE | ID: mdl-22371846
6.
Retroviral integrations in gene therapy trials.
Mol Ther
; 20(4): 709-16, 2012 Apr.
Article
in English
| MEDLINE | ID: mdl-22252453
7.
Tumor immunogenicity dictates reliance on TCF1 in CD8+ T cells for response to immunotherapy.
Cancer Cell
; 41(9): 1662-1679.e7, 2023 09 11.
Article
in English
| MEDLINE | ID: mdl-37625402
8.
Clonal expansion of T memory stem cells determines early anti-leukemic responses and long-term CAR T cell persistence in patients.
Nat Cancer
; 2(6): 629-642, 2021 06.
Article
in English
| MEDLINE | ID: mdl-34345830
9.
Long-term lymphoid progenitors independently sustain naïve T and NK cell production in humans.
Nat Commun
; 12(1): 1622, 2021 03 12.
Article
in English
| MEDLINE | ID: mdl-33712608
10.
Multilineage hematopoietic reconstitution without clonal selection in ADA-SCID patients treated with stem cell gene therapy.
J Clin Invest
; 117(8): 2233-40, 2007 Aug.
Article
in English
| MEDLINE | ID: mdl-17671653
11.
Lentiviral gene therapy for X-linked chronic granulomatous disease.
Nat Med
; 26(2): 200-206, 2020 02.
Article
in English
| MEDLINE | ID: mdl-31988463
12.
A comprehensive single cell transcriptional landscape of human hematopoietic progenitors.
Nat Commun
; 10(1): 2395, 2019 06 03.
Article
in English
| MEDLINE | ID: mdl-31160568
13.
Highly efficient therapeutic gene editing of human hematopoietic stem cells.
Nat Med
; 25(5): 776-783, 2019 05.
Article
in English
| MEDLINE | ID: mdl-30911135
14.
Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study.
Lancet Haematol
; 6(5): e239-e253, 2019 May.
Article
in English
| MEDLINE | ID: mdl-30981783
15.
Analyzing the Genotoxicity of Retroviral Vectors in Hematopoietic Cell Gene Therapy.
Mol Ther Methods Clin Dev
; 8: 21-30, 2018 Mar 16.
Article
in English
| MEDLINE | ID: mdl-29159200
16.
Dynamics of genetically engineered hematopoietic stem and progenitor cells after autologous transplantation in humans.
Nat Med
; 24(11): 1683-1690, 2018 11.
Article
in English
| MEDLINE | ID: mdl-30275570
17.
Successful hematopoietic stem cell mobilization and apheresis collection using plerixafor alone in sickle cell patients.
Blood Adv
; 2(19): 2505-2512, 2018 10 09.
Article
in English
| MEDLINE | ID: mdl-30282642
18.
Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE.
Mol Ther Methods Clin Dev
; 8: 152-165, 2018 Mar 16.
Article
in English
| MEDLINE | ID: mdl-29687034
19.
Integration Site Analysis in Gene Therapy Patients: Expectations and Reality.
Hum Gene Ther
; 28(12): 1122-1129, 2017 12.
Article
in English
| MEDLINE | ID: mdl-29160103
20.
Integrating Vectors for Gene Therapy and Clonal Tracking of Engineered Hematopoiesis.
Hematol Oncol Clin North Am
; 31(5): 737-752, 2017 10.
Article
in English
| MEDLINE | ID: mdl-28895844