Search details
1.
Myoediting: Toward Prevention of Muscular Dystrophy by Therapeutic Genome Editing.
Physiol Rev
; 98(3): 1205-1240, 2018 07 01.
Article
in English
| MEDLINE | ID: mdl-29717930
2.
Sorting of small RNAs into Arabidopsis argonaute complexes is directed by the 5' terminal nucleotide.
Cell
; 133(1): 116-27, 2008 Apr 04.
Article
in English
| MEDLINE | ID: mdl-18342361
3.
Ataxia and Purkinje cell degeneration in mice lacking the CAMTA1 transcription factor.
Proc Natl Acad Sci U S A
; 111(31): 11521-6, 2014 Aug 05.
Article
in English
| MEDLINE | ID: mdl-25049392
4.
Modeling and Correction of Protein Conformational Disease in iPSC-derived Neurons through Personalized Base Editing.
bioRxiv
; 2024 Jan 18.
Article
in English
| MEDLINE | ID: mdl-38293034
5.
Primate Model Carrying LMNA Mutation Develops Dilated Cardiomyopathy.
JACC Basic Transl Sci
; 9(3): 380-395, 2024 Mar.
Article
in English
| MEDLINE | ID: mdl-38559624
6.
Setting the pace of the Neurospora circadian clock by multiple independent FRQ phosphorylation events.
Proc Natl Acad Sci U S A
; 106(26): 10722-7, 2009 Jun 30.
Article
in English
| MEDLINE | ID: mdl-19506251
7.
A bacterial type III effector family uses the papain-like hydrolytic activity to arrest the host cell cycle.
Proc Natl Acad Sci U S A
; 106(10): 3716-21, 2009 Mar 10.
Article
in English
| MEDLINE | ID: mdl-19225106
8.
Two Prp19-like U-box proteins in the MOS4-associated complex play redundant roles in plant innate immunity.
PLoS Pathog
; 5(7): e1000526, 2009 Jul.
Article
in English
| MEDLINE | ID: mdl-19629177
9.
PINK1 gene mutation by pair truncated sgRNA/Cas9-D10A in cynomolgus monkeys.
Zool Res
; 42(4): 469-477, 2021 Jul 18.
Article
in English
| MEDLINE | ID: mdl-34213093
10.
Progress and challenges in CRISPR-mediated therapeutic genome editing for monogenic diseases.
J Biomed Res
; 35(2): 148-162, 2020 Nov 27.
Article
in English
| MEDLINE | ID: mdl-33402545
11.
Generation of a Hutchinson-Gilford progeria syndrome monkey model by base editing.
Protein Cell
; 11(11): 809-824, 2020 11.
Article
in English
| MEDLINE | ID: mdl-32729022
12.
In vivo non-invasive monitoring of dystrophin correction in a new Duchenne muscular dystrophy reporter mouse.
Nat Commun
; 10(1): 4537, 2019 10 04.
Article
in English
| MEDLINE | ID: mdl-31586095
13.
Correction of diverse muscular dystrophy mutations in human engineered heart muscle by single-site genome editing.
Sci Adv
; 4(1): eaap9004, 2018 01.
Article
in English
| MEDLINE | ID: mdl-29404407
14.
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
Sci Adv
; 3(4): e1602814, 2017 Apr.
Article
in English
| MEDLINE | ID: mdl-28439558
15.
Functional correction of dystrophin actin binding domain mutations by genome editing.
JCI Insight
; 2(18)2017 09 21.
Article
in English
| MEDLINE | ID: mdl-28931764
16.
Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy.
Sci Transl Med
; 9(418)2017 Nov 29.
Article
in English
| MEDLINE | ID: mdl-29187645
17.
Genome Editing of Monogenic Neuromuscular Diseases: A Systematic Review.
JAMA Neurol
; 73(11): 1349-1355, 2016 Nov 01.
Article
in English
| MEDLINE | ID: mdl-27668807
18.
Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy.
Science
; 351(6271): 400-3, 2016 Jan 22.
Article
in English
| MEDLINE | ID: mdl-26721683
19.
God does not play dice, and neither does CRISPR/Cas9.
Natl Sci Rev
; 6(3): 393, 2019 May.
Article
in English
| MEDLINE | ID: mdl-34691887
20.
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA.
Science
; 345(6201): 1184-1188, 2014 Sep 05.
Article
in English
| MEDLINE | ID: mdl-25123483