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One year outcome of boys with Duchenne muscular dystrophy using the Bayley-III scales of infant and toddler development.
Connolly, Anne M; Florence, Julaine M; Cradock, Mary M; Eagle, Michelle; Flanigan, Kevin M; McDonald, Craig M; Karachunski, Peter I; Darras, Basil T; Bushby, Kate; Malkus, Elizabeth C; Golumbek, Paul T; Zaidman, Craig M; Miller, J Philip; Mendell, Jerry R.
Affiliation
  • Connolly AM; Department of Neurology, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri; Department of Pediatrics, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri. Electronic address: con
  • Florence JM; Department of Neurology, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri.
  • Cradock MM; Department of Pediatrics, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri.
  • Eagle M; Department of Neurology, Newcastle University, Newcastle upon Tyne, England; Institute of Genetic Medicine, Newcastle University, Newcastle upon Tyne, England.
  • Flanigan KM; Departments of Pediatrics and Neurology, The Ohio State University, Columbus, Ohio; Gene Therapy Center, Nationwide Children's Hospital, Columbus, Ohio.
  • McDonald CM; Department Physical Medicine and Rehabilitation, University of California Davis Medical Center, University of California, Sacramento, California.
  • Karachunski PI; Department of Neurology, University of Minnesota, Minneapolis, Minnesota.
  • Darras BT; Department of Neurology, Boston Children's Hospital, Harvard University, Boston, Massachusetts.
  • Bushby K; Department of Neurology, Newcastle University, Newcastle upon Tyne, England; Institute of Genetic Medicine, Newcastle University, Newcastle upon Tyne, England.
  • Malkus EC; Department of Neurology, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri.
  • Golumbek PT; Department of Neurology, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri; Department of Pediatrics, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri.
  • Zaidman CM; Department of Neurology, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri; Department of Pediatrics, Saint Louis Children's Hospital, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri.
  • Miller JP; Division of Biostatistics, Washington University School of Medicine in Saint Louis, Saint Louis, Missouri.
  • Mendell JR; Departments of Pediatrics and Neurology, The Ohio State University, Columbus, Ohio; Gene Therapy Center, Nationwide Children's Hospital, Columbus, Ohio.
Pediatr Neurol ; 50(6): 557-63, 2014 Jun.
Article in En | MEDLINE | ID: mdl-24842254

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Child Development / Muscular Dystrophy, Duchenne Type of study: Clinical_trials / Observational_studies / Prognostic_studies Limits: Child, preschool / Humans / Infant / Male Language: En Journal: Pediatr Neurol Journal subject: NEUROLOGIA / PEDIATRIA Year: 2014 Type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Child Development / Muscular Dystrophy, Duchenne Type of study: Clinical_trials / Observational_studies / Prognostic_studies Limits: Child, preschool / Humans / Infant / Male Language: En Journal: Pediatr Neurol Journal subject: NEUROLOGIA / PEDIATRIA Year: 2014 Type: Article