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Time of Initiating Enzyme Replacement Therapy Affects Immune Abnormalities and Disease Severity in Patients with Gaucher Disease.
Limgala, Renuka Pudi; Ioanou, Chidima; Plassmeyer, Matthew; Ryherd, Mark; Kozhaya, Lina; Austin, Lauren; Abidoglu, Cem; Unutmaz, Derya; Alpan, Oral; Goker-Alpan, Ozlem.
Affiliation
  • Limgala RP; Lysosomal and Rare Disorders Research and Treatment Center, Fairfax, Virginia, United States of America.
  • Ioanou C; Amerimmune, O and O Alpan, LLC, Fairfax, Virginia, United States of America.
  • Plassmeyer M; Lysosomal and Rare Disorders Research and Treatment Center, Fairfax, Virginia, United States of America.
  • Ryherd M; Amerimmune, O and O Alpan, LLC, Fairfax, Virginia, United States of America.
  • Kozhaya L; Amerimmune, O and O Alpan, LLC, Fairfax, Virginia, United States of America.
  • Austin L; Jackson Laboratory for Genomic Medicine, Farmington, Connecticut, United States of America.
  • Abidoglu C; Amerimmune, O and O Alpan, LLC, Fairfax, Virginia, United States of America.
  • Unutmaz D; Jackson Laboratory for Genomic Medicine, Farmington, Connecticut, United States of America.
  • Alpan O; Jackson Laboratory for Genomic Medicine, Farmington, Connecticut, United States of America.
  • Goker-Alpan O; Amerimmune, O and O Alpan, LLC, Fairfax, Virginia, United States of America.
PLoS One ; 11(12): e0168135, 2016.
Article in En | MEDLINE | ID: mdl-27942037

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Enzyme Replacement Therapy / Time-to-Treatment / Gaucher Disease Limits: Adolescent / Adult / Aged / Child / Female / Humans / Male / Middle aged Language: En Journal: PLoS One Journal subject: CIENCIA / MEDICINA Year: 2016 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Enzyme Replacement Therapy / Time-to-Treatment / Gaucher Disease Limits: Adolescent / Adult / Aged / Child / Female / Humans / Male / Middle aged Language: En Journal: PLoS One Journal subject: CIENCIA / MEDICINA Year: 2016 Type: Article Affiliation country: United States