Your browser doesn't support javascript.
loading
Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.
Cox, Timothy M; Drelichman, Guillermo; Cravo, Renata; Balwani, Manisha; Burrow, Thomas Andrew; Martins, Ana Maria; Lukina, Elena; Rosenbloom, Barry; Goker-Alpan, Ozlem; Watman, Nora; El-Beshlawy, Amal; Kishnani, Priya S; Pedroso, Maria Lucia; Gaemers, Sebastiaan J M; Tayag, Regina; Peterschmitt, M Judith.
Affiliation
  • Cox TM; Department of Medicine, University of Cambridge, Addenbrooke's Hospital, Cambridge, United Kingdom.
  • Drelichman G; Hospital de Niños Ricardo Gutiérrez, Buenos Aires, Argentina.
  • Cravo R; State Institute of Haematology "Arthur de Siqueira Cavalcanti," Rio de Janeiro, Brazil.
  • Balwani M; Mount Sinai Hospital, New York, NY.
  • Burrow TA; Cincinnati Children's Hospital Medical Center, Cincinnati, OH.
  • Martins AM; Universidade Federal de São Paulo, São Paulo, Brazil.
  • Lukina E; National Research Center for Hematology, Moscow, Russia.
  • Rosenbloom B; Cedars-Sinai/Tower Hematology Oncology, Beverly Hills, CA.
  • Goker-Alpan O; Lysosomal Disorders Unit, O&O Alpan, LLC, Fairfax, VA.
  • Watman N; Hospital Ramos Mejia, Buenos Aires, Argentina.
  • El-Beshlawy A; Pediatric Hematology, Cairo University, Cairo, Egypt.
  • Kishnani PS; Department of Pediatrics, Duke University School of Medicine, Durham, NC.
  • Pedroso ML; Gastroenterology Department, Universidade Federal do Paraná, Curitiba, Brazil.
  • Gaemers SJM; Sanofi Genzyme, Cambridge, MA; and.
  • Tayag R; Prometrika LLC, Cambridge, MA.
  • Peterschmitt MJ; Sanofi Genzyme, Cambridge, MA; and.
Blood ; 129(17): 2375-2383, 2017 04 27.
Article in En | MEDLINE | ID: mdl-28167660
Subject(s)
Fulltext
Print
XML
PubMed Links
Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Pyrrolidines / Recombinant Proteins / Enzyme Inhibitors / Enzyme Replacement Therapy / Gaucher Disease / Glucosylceramidase Type of study: Clinical_trials / Prognostic_studies Limits: Adult / Female / Humans / Male / Middle aged Language: En Journal: Blood Year: 2017 Type: Article Affiliation country: United kingdom
Fulltext
Print
XML
PubMed Links
Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Pyrrolidines / Recombinant Proteins / Enzyme Inhibitors / Enzyme Replacement Therapy / Gaucher Disease / Glucosylceramidase Type of study: Clinical_trials / Prognostic_studies Limits: Adult / Female / Humans / Male / Middle aged Language: En Journal: Blood Year: 2017 Type: Article Affiliation country: United kingdom