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Gene therapy with adeno-associated virus vector 5-human factor IX in adults with hemophilia B.
Miesbach, Wolfgang; Meijer, Karina; Coppens, Michiel; Kampmann, Peter; Klamroth, Robert; Schutgens, Roger; Tangelder, Marco; Castaman, Giancarlo; Schwäble, Joachim; Bonig, Halvard; Seifried, Erhard; Cattaneo, Federica; Meyer, Christian; Leebeek, Frank W G.
Affiliation
  • Miesbach W; University Hospital Frankfurt, Frankfurt, Germany.
  • Meijer K; University Medical Centre Groningen, University of Groningen, Groningen, The Netherlands.
  • Coppens M; Academic Medical Center, Amsterdam, The Netherlands.
  • Kampmann P; Rigshospitalet, Copenhagen, Denmark.
  • Klamroth R; Vivantes Klinikum, Berlin, Germany.
  • Schutgens R; University Medical Centre Utrecht and University Utrecht, Utrecht, The Netherlands.
  • Tangelder M; uniQure biopharma B.V., Amsterdam, The Netherlands.
  • Castaman G; Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
  • Schwäble J; Institute for Transfusion Medicine and Immunohematology, Goethe University Hospital Medical School, German Red Cross Blood Donor Service, Frankfurt, Germany.
  • Bonig H; Institute for Transfusion Medicine and Immunohematology, Goethe University Hospital Medical School, German Red Cross Blood Donor Service, Frankfurt, Germany.
  • Seifried E; Department of Medicine/Hematology, University of Washington, Seattle, WA.
  • Cattaneo F; Institute for Transfusion Medicine and Immunohematology, Goethe University Hospital Medical School, German Red Cross Blood Donor Service, Frankfurt, Germany.
  • Meyer C; Chiesi Farmaceutici S.p.A., Parma, Italy; and.
  • Leebeek FWG; uniQure biopharma B.V., Amsterdam, The Netherlands.
Blood ; 131(9): 1022-1031, 2018 03 01.
Article in En | MEDLINE | ID: mdl-29246900

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Factor IX / Prednisolone / Genetic Therapy / Hemophilia B / Parvovirinae / Genetic Vectors Type of study: Clinical_trials / Risk_factors_studies Limits: Adult / Female / Humans / Male Language: En Journal: Blood Year: 2018 Type: Article Affiliation country: Germany

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Factor IX / Prednisolone / Genetic Therapy / Hemophilia B / Parvovirinae / Genetic Vectors Type of study: Clinical_trials / Risk_factors_studies Limits: Adult / Female / Humans / Male Language: En Journal: Blood Year: 2018 Type: Article Affiliation country: Germany