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Morpholino-induced exon skipping stimulates cell-mediated and humoral responses to dystrophin in mdx mice.
Vila, Maria C; Novak, James S; Benny Klimek, Margaret; Li, Ning; Morales, Melissa; Fritz, Alexander G; Edwards, Katie; Boehler, Jessica F; Hogarth, Marshall W; Kinder, Travis B; Zhang, Aiping; Mazala, Davi; Fiorillo, Alyson A; Douglas, Bonnie; Chen, Yi-Wen; van den Anker, John; Lu, Qi L; Hathout, Yetrib; Hoffman, Eric P; Partridge, Terence A; Nagaraju, Kanneboyina.
Affiliation
  • Vila MC; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • Novak JS; Institute for Biomedical Sciences, The George Washington University, School of Medicine and Health Sciences, Washington, DC, USA.
  • Benny Klimek M; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • Li N; Institute for Biomedical Sciences, The George Washington University, School of Medicine and Health Sciences, Washington, DC, USA.
  • Morales M; Department of Genomics and Precision Medicine, The George Washington University, School of Medicine and Health Sciences, Washington, DC, USA.
  • Fritz AG; Department of Pediatrics, The George Washington University, School of Medicine and Health Sciences, Washington, DC, USA.
  • Edwards K; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • Boehler JF; Department of Pharmaceutical Sciences, School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Hogarth MW; Department of Pharmaceutical Sciences, School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Kinder TB; Department of Pharmaceutical Sciences, School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Zhang A; Department of Pharmaceutical Sciences, School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Mazala D; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • Fiorillo AA; Institute for Biomedical Sciences, The George Washington University, School of Medicine and Health Sciences, Washington, DC, USA.
  • Douglas B; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • Chen YW; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • van den Anker J; Institute for Biomedical Sciences, The George Washington University, School of Medicine and Health Sciences, Washington, DC, USA.
  • Lu QL; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • Hathout Y; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • Hoffman EP; Center for Genetic Medicine, Children's National Health System, Washington, DC, USA.
  • Partridge TA; Institute for Biomedical Sciences, The George Washington University, School of Medicine and Health Sciences, Washington, DC, USA.
  • Nagaraju K; Department of Genomics and Precision Medicine, The George Washington University, School of Medicine and Health Sciences, Washington, DC, USA.
J Pathol ; 248(3): 339-351, 2019 07.
Article in En | MEDLINE | ID: mdl-30883742

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Exons / Dystrophin / Muscular Dystrophy, Duchenne / Morpholinos Limits: Animals Language: En Journal: J Pathol Year: 2019 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Exons / Dystrophin / Muscular Dystrophy, Duchenne / Morpholinos Limits: Animals Language: En Journal: J Pathol Year: 2019 Type: Article Affiliation country: United States