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Mucopolysaccharidosis IVA: Diagnosis, Treatment, and Management.
Sawamoto, Kazuki; Álvarez González, José Víctor; Piechnik, Matthew; Otero, Francisco J; Couce, Maria L; Suzuki, Yasuyuki; Tomatsu, Shunji.
Affiliation
  • Sawamoto K; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE 19803, USA.
  • Álvarez González JV; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE 19803, USA.
  • Piechnik M; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE 19803, USA.
  • Otero FJ; University of Delaware, Newark, DE 19716, USA.
  • Couce ML; Department of Pharmacology, Pharmacy and Pharmaceutical Technology, School of Pharmacy, University of Santiago de Compostela, 15872 Santiago de Compostela, Spain.
  • Suzuki Y; Department of Forensic Sciences, Pathology, Gynecology and Obstetrics and Pediatrics Neonatology Service, Metabolic Unit, IDIS, CIBERER, MetabERN, University Clinic Hospital of Santiago de Compostela, 15706 Santiago de Compostela, Spain.
  • Tomatsu S; Department of Pediatrics, Graduate School of Medicine, Gifu University, Gifu 501-1193, Japan.
Int J Mol Sci ; 21(4)2020 Feb 23.
Article in En | MEDLINE | ID: mdl-32102177

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Mucopolysaccharidosis IV / Disease Management Type of study: Diagnostic_studies / Screening_studies Limits: Humans Language: En Journal: Int J Mol Sci Year: 2020 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Mucopolysaccharidosis IV / Disease Management Type of study: Diagnostic_studies / Screening_studies Limits: Humans Language: En Journal: Int J Mol Sci Year: 2020 Type: Article Affiliation country: United States