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Huntingtin-Lowering Therapies for Huntington Disease: A Review of the Evidence of Potential Benefits and Risks.
Leavitt, Blair R; Kordasiewicz, Holly B; Schobel, Scott A.
Affiliation
  • Leavitt BR; Department of Medical Genetics, Centre for Molecular Medicine and Therapeutics, BC Children's Hospital, University of British Columbia, Vancouver, British Columbia, Canada.
  • Kordasiewicz HB; Ionis Pharmaceuticals, Carlsbad, California.
  • Schobel SA; F. Hoffmann-La Roche Ltd, Basel, Switzerland.
JAMA Neurol ; 77(6): 764-772, 2020 06 01.
Article in En | MEDLINE | ID: mdl-32202594

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Oligonucleotides, Antisense / Huntington Disease / Huntingtin Protein Type of study: Etiology_studies / Risk_factors_studies / Systematic_reviews Limits: Animals / Humans Language: En Journal: JAMA Neurol Year: 2020 Type: Article Affiliation country: Canada

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Oligonucleotides, Antisense / Huntington Disease / Huntingtin Protein Type of study: Etiology_studies / Risk_factors_studies / Systematic_reviews Limits: Animals / Humans Language: En Journal: JAMA Neurol Year: 2020 Type: Article Affiliation country: Canada