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Dose Range Finding Studies with Two RPGR Transgenes in a Canine Model of X-Linked Retinitis Pigmentosa Treated with Subretinal Gene Therapy.
Song, Chunjuan; Dufour, Valérie L; Cideciyan, Artur V; Ye, Guo-Jie; Swider, Malgorzata; Newmark, Judith A; Timmers, Adrian M; Robinson, Paulette M; Knop, David R; Chulay, Jeffrey D; Jacobson, Samuel G; Aguirre, Gustavo D; Beltran, William A; Shearman, Mark S.
Affiliation
  • Song C; Applied Genetic Technologies Corporation, Alachua, Florida, USA.
  • Dufour VL; Division of Experimental Retinal Therapies, Department of Clinical Sciences & Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Cideciyan AV; Department of Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA.
  • Ye GJ; Applied Genetic Technologies Corporation, Alachua, Florida, USA.
  • Swider M; Department of Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA.
  • Newmark JA; Applied Genetic Technologies Corporation, Alachua, Florida, USA.
  • Timmers AM; Applied Genetic Technologies Corporation, Alachua, Florida, USA.
  • Robinson PM; Applied Genetic Technologies Corporation, Alachua, Florida, USA.
  • Knop DR; Applied Genetic Technologies Corporation, Alachua, Florida, USA.
  • Chulay JD; Applied Genetic Technologies Corporation, Alachua, Florida, USA.
  • Jacobson SG; Department of Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA.
  • Aguirre GD; Division of Experimental Retinal Therapies, Department of Clinical Sciences & Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Beltran WA; Division of Experimental Retinal Therapies, Department of Clinical Sciences & Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Shearman MS; Applied Genetic Technologies Corporation, Alachua, Florida, USA.
Hum Gene Ther ; 31(13-14): 743-755, 2020 07.
Article in En | MEDLINE | ID: mdl-32414297

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Retinitis Pigmentosa / Dependovirus / Genetic Diseases, X-Linked / Eye Proteins / Genetic Vectors / Mutation Limits: Animals Language: En Journal: Hum Gene Ther Journal subject: GENETICA MEDICA / TERAPEUTICA Year: 2020 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Retinitis Pigmentosa / Dependovirus / Genetic Diseases, X-Linked / Eye Proteins / Genetic Vectors / Mutation Limits: Animals Language: En Journal: Hum Gene Ther Journal subject: GENETICA MEDICA / TERAPEUTICA Year: 2020 Type: Article Affiliation country: United States