Intracranial delivery of AAV9 gene therapy partially prevents retinal degeneration and visual deficits in CLN6-Batten disease mice.
Mol Ther Methods Clin Dev
; 20: 497-507, 2021 Mar 12.
Article
in En
| MEDLINE
| ID: mdl-33665223
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Language:
En
Journal:
Mol Ther Methods Clin Dev
Year:
2021
Type:
Article
Affiliation country:
United States