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Cell type-selective targeted delivery of a recombinant lysosomal enzyme for enzyme therapies.
Baik, Andrew D; Calafati, Philip; Zhang, Xiaoli; Aaron, Nina A; Mehra, Antonia; Moller-Tank, Sven; Miloscio, Lawrence; Praggastis, Maria; Giovannone, Nicholas; Pan, Cheryl; Tang, Yajun; Bridges, Susannah; Mujica, Alejo; Barbounis, Peter; Yanolatos, Jean; Gale, Nicholas; Li, Ning; Kyratsous, Christos A; Schoenherr, Christopher J; Murphy, Andrew J; Economides, Aris N; Cygnar, Katherine D.
Affiliation
  • Baik AD; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Calafati P; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Zhang X; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Aaron NA; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Mehra A; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Moller-Tank S; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Miloscio L; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Praggastis M; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Giovannone N; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Pan C; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Tang Y; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Bridges S; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Mujica A; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Barbounis P; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Yanolatos J; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Gale N; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Li N; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Kyratsous CA; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Schoenherr CJ; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Murphy AJ; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA.
  • Economides AN; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA. Electronic address: aris.economides@regeneron.com.
  • Cygnar KD; Regeneron Pharmaceuticals, Tarrytown, NY 10591, USA. Electronic address: katherine.cygnar@regeneron.com.
Mol Ther ; 29(12): 3512-3524, 2021 12 01.
Article in En | MEDLINE | ID: mdl-34400331

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Storage Disease Type II / Lysosomal Storage Diseases Limits: Animals Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2021 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Storage Disease Type II / Lysosomal Storage Diseases Limits: Animals Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2021 Type: Article Affiliation country: United States