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CRISPR/Cas9 PIG -A gene editing in nonhuman primate model demonstrates no intrinsic clonal expansion of PNH HSPCs.
Shin, Tae-Hoon; Baek, Eun Jung; Corat, Marcus A F; Chen, Shirley; Metais, Jean-Yves; AlJanahi, Aisha A; Zhou, Yifan; Donahue, Robert E; Yu, Kyung-Rok; Dunbar, Cynthia E.
Afiliación
  • Shin TH; Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD.
  • Baek EJ; Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD.
  • Corat MAF; Department of Laboratory Medicine, College of Medicine, Hanyang University, Seoul, Republic of Korea.
  • Chen S; Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD.
  • Metais JY; Multidisciplinary Center for Biological Research, University of Campinas, Campinas, Brazil.
  • AlJanahi AA; Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD.
  • Zhou Y; Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD.
  • Donahue RE; Department of Bone Marrow Transplantation and Cellular Therapy, St. Jude Children's Research Hospital, Memphis, TN; and.
  • Yu KR; Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD.
  • Dunbar CE; Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD.
Blood ; 133(23): 2542-2545, 2019 06 06.
Article en En | MEDLINE | ID: mdl-31003997

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Células Madre Hematopoyéticas / Modelos Animales de Enfermedad / Hemoglobinuria Paroxística / Proteínas de la Membrana Límite: Animals Idioma: En Revista: Blood Año: 2019 Tipo del documento: Article País de afiliación: Moldova

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Células Madre Hematopoyéticas / Modelos Animales de Enfermedad / Hemoglobinuria Paroxística / Proteínas de la Membrana Límite: Animals Idioma: En Revista: Blood Año: 2019 Tipo del documento: Article País de afiliación: Moldova