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A Molecular Revolution in the Treatment of Hemophilia.
Butterfield, John S S; Hege, Kerry M; Herzog, Roland W; Kaczmarek, Radoslaw.
Afiliación
  • Butterfield JSS; Department of Pediatrics, University of Florida, Gainesville, FL, USA.
  • Hege KM; Department of Pediatrics, Indiana University School of Medicine, IUPUI-Wells Center for Pediatric Research, Indianapolis, IN, USA.
  • Herzog RW; Department of Pediatrics, University of Florida, Gainesville, FL, USA; Department of Pediatrics, Indiana University School of Medicine, IUPUI-Wells Center for Pediatric Research, Indianapolis, IN, USA. Electronic address: rwherzog@iu.edu.
  • Kaczmarek R; Department of Pediatrics, Indiana University School of Medicine, IUPUI-Wells Center for Pediatric Research, Indianapolis, IN, USA; Laboratory of Glycobiology, Hirszfeld Institute of Immunology and Experimental Therapy, Wroclaw, Poland. Electronic address: rkaczmar@iu.edu.
Mol Ther ; 28(4): 997-1015, 2020 04 08.
Article en En | MEDLINE | ID: mdl-31843450

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Hemofilia B / Anticuerpos Biespecíficos / ARN Interferente Pequeño / Hemofilia A Tipo de estudio: Prognostic_studies Límite: Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2020 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Hemofilia B / Anticuerpos Biespecíficos / ARN Interferente Pequeño / Hemofilia A Tipo de estudio: Prognostic_studies Límite: Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2020 Tipo del documento: Article País de afiliación: Estados Unidos