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Small circular interfering RNAs (sciRNAs) as a potent therapeutic platform for gene-silencing.
Jahns, Hartmut; Degaonkar, Rohan; Podbevsek, Peter; Gupta, Swati; Bisbe, Anna; Aluri, Krishna; Szeto, John; Kumar, Pawan; LeBlanc, Sarah; Racie, Tim; Brown, Christopher R; Castoreno, Adam; Guenther, Dale C; Jadhav, Vasant; Maier, Martin A; Plavec, Janez; Egli, Martin; Manoharan, Muthiah; Zlatev, Ivan.
Afiliación
  • Jahns H; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Degaonkar R; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Podbevsek P; Slovenian NMR Center, National Institute of Chemistry, Hajdrihova 19, SI-1001 Ljubljana, Slovenia, EU.
  • Gupta S; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Bisbe A; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Aluri K; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Szeto J; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Kumar P; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • LeBlanc S; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Racie T; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Brown CR; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Castoreno A; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Guenther DC; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Jadhav V; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Maier MA; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Plavec J; Slovenian NMR Center, National Institute of Chemistry, Hajdrihova 19, SI-1001 Ljubljana, Slovenia, EU.
  • Egli M; Department of Biochemistry, School of Medicine, Vanderbilt University, Nashville, TN 37232, USA.
  • Manoharan M; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
  • Zlatev I; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA.
Nucleic Acids Res ; 49(18): 10250-10264, 2021 10 11.
Article en En | MEDLINE | ID: mdl-34508350

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Silenciador del Gen / ARN Interferente Pequeño / Interferencia de ARN / ARN Circular Límite: Animals Idioma: En Revista: Nucleic Acids Res Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Silenciador del Gen / ARN Interferente Pequeño / Interferencia de ARN / ARN Circular Límite: Animals Idioma: En Revista: Nucleic Acids Res Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos