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Design and outcome measures of LAVENDER, a phase 3 study of trofinetide for Rett syndrome.
Neul, Jeffrey L; Percy, Alan K; Benke, Timothy A; Berry-Kravis, Elizabeth M; Glaze, Daniel G; Peters, Sarika U; Jones, Nancy E; Youakim, James M.
Afiliación
  • Neul JL; Vanderbilt Kennedy Center, Vanderbilt University Medical Center, Nashville, TN, United States. Electronic address: jeffrey.l.neul@vumc.org.
  • Percy AK; University of Alabama at Birmingham, Birmingham, AL, United States. Electronic address: apercy@uabmc.com.
  • Benke TA; Children's Hospital of Colorado/University of Colorado School of Medicine, Aurora, CO, United States. Electronic address: tim.benke@cuanschutz.edu.
  • Berry-Kravis EM; Rush University Children's Hospital, Chicago, IL, United States. Electronic address: elizabeth_berry-kravis@rush.edu.
  • Glaze DG; Texas Children's Hospital/Baylor College of Medicine, Houston, TX, United States. Electronic address: dglaze@bcm.edu.
  • Peters SU; Vanderbilt Kennedy Center, Vanderbilt University Medical Center, Nashville, TN, United States. Electronic address: sarika.u.peters@vumc.org.
  • Jones NE; Neuren Pharmaceuticals Limited, Melbourne, Australia. Electronic address: njones@neurenpharma.com.
  • Youakim JM; Acadia Pharmaceuticals Inc., Princeton, NJ, United States. Electronic address: jyouakim@ACADIA-Pharm.com.
Contemp Clin Trials ; 114: 106704, 2022 03.
Article en En | MEDLINE | ID: mdl-35149233

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Síndrome de Rett Tipo de estudio: Clinical_trials Límite: Adolescent / Child / Child, preschool / Female / Humans Idioma: En Revista: Contemp Clin Trials Asunto de la revista: MEDICINA / TERAPEUTICA Año: 2022 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Síndrome de Rett Tipo de estudio: Clinical_trials Límite: Adolescent / Child / Child, preschool / Female / Humans Idioma: En Revista: Contemp Clin Trials Asunto de la revista: MEDICINA / TERAPEUTICA Año: 2022 Tipo del documento: Article