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Childhood-onset Erdheim-Chester disease in the molecular era: clinical phenotypes and long-term outcomes of 21 patients.
Pegoraro, Francesco; Mazzariol, Martina; Trambusti, Irene; Bakhshi, Sameer; Mallick, Saumyaranjan; Dunkel, Ira J; van den Bos, Cor; Tezol, Özlem; Shan, Shijun; Ocak, Suheyla; Giordano, Flavio; De Fusco, Carmela; Gaspari, Stefania; Buccoliero, Anna Maria; Coniglio, Maria Luisa; Buti, Elisa; Romagnani, Paola; Picarsic, Jennifer; Donadieu, Jean; Diamond, Eli L; Emile, Jean-François; Sieni, Elena; Haroche, Julien; Vaglio, Augusto.
Afiliación
  • Pegoraro F; Department of Health Sciences, University of Florence, Florence, Italy.
  • Mazzariol M; Hematology and Oncology Unit, Meyer Children's Hospital Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), Florence, Italy.
  • Trambusti I; Department of Medical Sciences, University of Turin, Turin, Italy.
  • Bakhshi S; Nephrology and Dialysis Unit, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Mallick S; Hematology and Oncology Unit, Meyer Children's Hospital Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), Florence, Italy.
  • Dunkel IJ; Department of Clinical and Experimental Medicine, University of Pisa, Pisa, Italy.
  • van den Bos C; Department of Medical Oncology, All India Institute of Medical Sciences, New Delhi, India.
  • Tezol Ö; Department of Pathology, All India Institute of Medical Sciences, New Delhi, India.
  • Shan S; Department of Pediatrics, Memorial Sloan Kettering Cancer Center, New York, NY.
  • Ocak S; Department of Hemato-Oncology, Princess Máxima Center for Pediatric Oncology, Utrecht, The Netherlands.
  • Giordano F; Department of Pediatrics, Mersin University Faculty of Medicine, Mersin, Turkey.
  • De Fusco C; Department of Dermatology, No. 1 Hospital of China Medical University, Shenyang, China.
  • Gaspari S; Department of Pediatric Hematology-Oncology, Istanbul University Cerrahpasa, Cerrahpasa Faculty of Medicine, Istanbul, Turkey.
  • Buccoliero AM; Department of Neurosurgery, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Coniglio ML; NEUROFARBA Department, University of Florence, Florence, Italy.
  • Buti E; Department of Oncology, Azienda Ospedaliera di Rilievo Nazionale Santobono-Pausilipon, Pausilipon Hospital, Naples, Italy.
  • Romagnani P; Department of Pediatric Hematology/Oncology, Cellular and Gene Therapy, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.
  • Picarsic J; Pathology Unit, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Donadieu J; Hematology and Oncology Unit, Meyer Children's Hospital Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), Florence, Italy.
  • Diamond EL; Nephrology and Dialysis Unit, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Emile JF; Nephrology and Dialysis Unit, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Sieni E; Department of Biomedical, Experimental and Clinical Sciences "Mario Serio," University of Florence, Florence, Italy.
  • Haroche J; Cincinnati Children's Hospital Medical Center, University of Cincinnati School of Medicine, Cincinnati, OH.
  • Vaglio A; Pediatric Oncology and Hematology, Armand-Trousseau Hospital, Assistance Publique-Hôpitaux de Paris, EA4340-BECCOH, Referral Center for Histiocytoses Université de Versailles Saint-Quentin-en-Yvelines, Paris, France.
Blood ; 142(13): 1167-1171, 2023 09 28.
Article en En | MEDLINE | ID: mdl-37490651

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Enfermedad de Erdheim-Chester Límite: Child / Humans Idioma: En Revista: Blood Año: 2023 Tipo del documento: Article País de afiliación: Italia

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Enfermedad de Erdheim-Chester Límite: Child / Humans Idioma: En Revista: Blood Año: 2023 Tipo del documento: Article País de afiliación: Italia