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Current Clinical Applications of In Vivo Gene Therapy with AAVs.
Mendell, Jerry R; Al-Zaidy, Samiah A; Rodino-Klapac, Louise R; Goodspeed, Kimberly; Gray, Steven J; Kay, Christine N; Boye, Sanford L; Boye, Shannon E; George, Lindsey A; Salabarria, Stephanie; Corti, Manuela; Byrne, Barry J; Tremblay, Jacques P.
Afiliación
  • Mendell JR; Center of Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, OH, USA; Department of Pediatrics and Neurology, The Ohio State University, Columbus, OH, USA.
  • Al-Zaidy SA; Al-Zaidy and Associates, LLC, Columbus, OH, USA.
  • Rodino-Klapac LR; Sarepta Therapeutics, Inc., Cambridge, MA, USA.
  • Goodspeed K; Department of Pediatrics, UT Southwestern Medical Center, Dallas, TX, USA.
  • Gray SJ; Department of Pediatrics, UT Southwestern Medical Center, Dallas, TX, USA.
  • Kay CN; Vitreoretinal Associates, Gainesville, FL, USA.
  • Boye SL; Department of Pediatrics, Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA.
  • Boye SE; Division of Cellular and Molecular Therapeutics, University of Florida, Gainesville, FL, USA.
  • George LA; Division of Hematology and the Perelman Center for Cellular and Molecular Therapeutics, Philadelphia, PA, USA; Children's Hospital of Philadelphia, Philadelphia, PA, USA.
  • Salabarria S; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA, USA.
  • Corti M; Department of Pediatrics, College of Medicine, University of Florida, Gainesville, FL, USA; Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA.
  • Byrne BJ; Department of Pediatrics, College of Medicine, University of Florida, Gainesville, FL, USA; Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA.
  • Tremblay JP; Centre de Recherche du CHUQ-Université Laval, Québec, QC, Canada. Electronic address: jacques-p.tremblay@crchul.ulaval.ca.
Mol Ther ; 29(2): 464-488, 2021 02 03.
Article en En | MEDLINE | ID: mdl-33309881
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Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Dependovirus / Vectores Genéticos Límite: Animals / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos
Texto completo
Imprimir
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PubMed Links
Buscar en Google

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Dependovirus / Vectores Genéticos Límite: Animals / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos