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An examination of the efficacy and safety of fenfluramine in adults, children, and adolescents with Dravet syndrome in a real-world practice setting: A report from the Fenfluramine European Early Access Program.
Guerrini, Renzo; Specchio, Nicola; Aledo-Serrano, Ángel; Pringsheim, Milka; Darra, Francesca; Mayer, Thomas; Gil-Nagel, Antonio; Polster, Tilman; Zuberi, Sameer M; Lothe, Amélie; Gammaitoni, Arnold; Strzelczyk, Adam.
Afiliación
  • Guerrini R; Children's Hospital A Meyer, University of Florence, Full Member of European Reference Network on Rare and Complex Epilepsies EpiCARE, Florence, Italy.
  • Specchio N; Rare and Complex Epilepsy Unit, Department of Neuroscience, Bambino Gesù Children's Hospital IRCCS, Full Member of European Reference Network on Rare and Complex Epilepsies EpiCARE, Rome, Italy.
  • Aledo-Serrano Á; Epilepsy Program, Department of Neurology, Hospital Ruber Internacional, Madrid, Spain.
  • Pringsheim M; Clinic for Neuropediatrics and Neurorehabilitation, Epilepsy Center for Children and Adolescents, Schön Klinik, Vogtareuth, Germany.
  • Darra F; Department for Congenital Heart Disease and Pediatric Cardiology, German Heart Center, Munich, Germany.
  • Mayer T; Research Institute for Rehabilitation, Transition and Palliation, Paracelsus Medical University, Salzburg, Austria.
  • Gil-Nagel A; Child Neuropsychiatry, Department of Surgical Sciences, Dentistry, Gynecology and Pediatrics, University of Verona, Full Member of European Reference Network on Rare and Complex Epilepsies EpiCARE, Verona, Italy.
  • Polster T; Epilepsy Center Kleinwachau, Dresden-Radeberg, Germany.
  • Zuberi SM; Epilepsy Program, Department of Neurology, Hospital Ruber Internacional, Madrid, Spain.
  • Lothe A; Krankenhaus Mara - Bethel Epilepsy Centre, Department of Epileptology, Medical School, Bielefeld University, Bielefeld, Germany.
  • Gammaitoni A; Paediatric Neurosciences Research Group, Royal Hospital for Children & Institute of Health & Wellbeing, University of Glasgow, Glasgow, UK.
  • Strzelczyk A; Zogenix International, Maidenhead, UK.
Epilepsia Open ; 7(4): 578-587, 2022 12.
Article en En | MEDLINE | ID: mdl-35801621

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Epilepsias Mioclónicas / Fenfluramina Límite: Adolescent / Adult / Child / Humans Idioma: En Revista: Epilepsia Open Año: 2022 Tipo del documento: Article País de afiliación: Italia

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Epilepsias Mioclónicas / Fenfluramina Límite: Adolescent / Adult / Child / Humans Idioma: En Revista: Epilepsia Open Año: 2022 Tipo del documento: Article País de afiliación: Italia