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Long-term treatment with eteplirsen in nonambulatory patients with Duchenne muscular dystrophy.
Alfano, Lindsay N; Charleston, Jay S; Connolly, Anne M; Cripe, Linda; Donoghue, Cas; Dracker, Robert; Dworzak, Johannes; Eliopoulos, Helen; Frank, Diane E; Lewis, Sarah; Lucas, Karin; Lynch, Jessie; Milici, A J; Flynt, Amy; Naughton, Emily; Rodino-Klapac, Louise R; Sahenk, Zarife; Schnell, Frederick J; Young, G David; Mendell, Jerry R; Lowes, Linda P.
Afiliación
  • Alfano LN; Pediatrics, Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH.
  • Charleston JS; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Connolly AM; Currently: Pediatrics, Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH.
  • Cripe L; Department of Neurology, Washington University School of Medicine, St. Louis, MO.
  • Donoghue C; Pediatrics, Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH.
  • Dracker R; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Dworzak J; Summerwood Pediatrics/Infusacare Medical Services, PC, Liverpool, NY.
  • Eliopoulos H; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Frank DE; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Lewis S; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Lucas K; Pediatrics, Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH.
  • Lynch J; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Milici AJ; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Flynt A; Flagship Biosciences, Westminster, CO.
  • Naughton E; PharPoint Research, Durham, NC.
  • Rodino-Klapac LR; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Sahenk Z; Pediatrics, Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH.
  • Schnell FJ; Currently: Sarepta Therapeutics, Inc., Cambridge, MA, USA.
  • Young GD; Pediatrics, Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH.
  • Mendell JR; Sarepta Therapeutics, Inc., Cambridge, MA.
  • Lowes LP; Flagship Biosciences, Westminster, CO.
Medicine (Baltimore) ; 98(26): e15858, 2019 Jun.
Article en En | MEDLINE | ID: mdl-31261494

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Distrofia Muscular de Duchenne / Morfolinos Tipo de estudio: Clinical_trials Límite: Child / Humans / Male Idioma: En Revista: Medicine (Baltimore) Año: 2019 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Distrofia Muscular de Duchenne / Morfolinos Tipo de estudio: Clinical_trials Límite: Child / Humans / Male Idioma: En Revista: Medicine (Baltimore) Año: 2019 Tipo del documento: Article