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Natural progression of cardiac features and long-term effects of enzyme replacement therapy in Taiwanese patients with mucopolysaccharidosis II.
Lin, Hsiang-Yu; Chen, Ming-Ren; Lee, Chung-Lin; Lin, Shan-Miao; Hung, Chung-Lieh; Niu, Dau-Ming; Chang, Tung-Ming; Chuang, Chih-Kuang; Lin, Shuan-Pei.
Afiliación
  • Lin HY; Department of Medicine, MacKay Medical College, New Taipei City, Taiwan.
  • Chen MR; Department of Pediatrics, MacKay Memorial Hospital, No.92, Sec. 2, Chung-Shan North Road, Taipei, 10449, Taiwan.
  • Lee CL; Department of Medical Research, MacKay Memorial Hospital, 92 Chung-Shan N. Rd., Sec. 2, Taipei, 10449, Taiwan.
  • Lin SM; Department of Childhood Care and Education, MacKay Junior College of Medicine, Nursing and Management, Taipei, Taiwan.
  • Hung CL; Department of Medical Research, China Medical University Hospital, China Medical University, Taichung, Taiwan.
  • Niu DM; Department of Rare Disease Center, MacKay Memorial Hospital, Taipei, Taiwan.
  • Chang TM; Department of Medicine, MacKay Medical College, New Taipei City, Taiwan.
  • Chuang CK; Department of Pediatrics, MacKay Memorial Hospital, No.92, Sec. 2, Chung-Shan North Road, Taipei, 10449, Taiwan.
  • Lin SP; Department of Childhood Care and Education, MacKay Junior College of Medicine, Nursing and Management, Taipei, Taiwan.
Orphanet J Rare Dis ; 16(1): 99, 2021 02 23.
Article en En | MEDLINE | ID: mdl-33622387

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Mucopolisacaridosis II / Enfermedades de las Válvulas Cardíacas Tipo de estudio: Prognostic_studies / Risk_factors_studies Límite: Adolescent / Adult / Child / Child, preschool / Humans / Infant Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2021 Tipo del documento: Article País de afiliación: Taiwán

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Mucopolisacaridosis II / Enfermedades de las Válvulas Cardíacas Tipo de estudio: Prognostic_studies / Risk_factors_studies Límite: Adolescent / Adult / Child / Child, preschool / Humans / Infant Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2021 Tipo del documento: Article País de afiliación: Taiwán