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Exon-skipping antisense oligonucleotides for cystic fibrosis therapy.
Kim, Young Jin; Sivetz, Nicole; Layne, Jessica; Voss, Dillon M; Yang, Lucia; Zhang, Qian; Krainer, Adrian R.
Afiliación
  • Kim YJ; Cold Spring Harbor Laboratory, Cold Spring Harbor, NY 11724.
  • Sivetz N; Graduate Program in Genetics, Stony Brook University, Stony Brook, NY 11794.
  • Layne J; Medical Scientist Training Program, Stony Brook University School of Medicine, Stony Brook, NY 11794.
  • Voss DM; Cold Spring Harbor Laboratory, Cold Spring Harbor, NY 11724.
  • Yang L; Cold Spring Harbor Laboratory, Cold Spring Harbor, NY 11724.
  • Zhang Q; Cold Spring Harbor Laboratory, Cold Spring Harbor, NY 11724.
  • Krainer AR; Graduate Program in Genetics, Stony Brook University, Stony Brook, NY 11794.
Proc Natl Acad Sci U S A ; 119(3)2022 01 18.
Article en En | MEDLINE | ID: mdl-35017301

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Terapia Genética / Exones / Oligonucleótidos Antisentido / Fibrosis Quística Límite: Humans Idioma: En Revista: Proc Natl Acad Sci U S A Año: 2022 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Terapia Genética / Exones / Oligonucleótidos Antisentido / Fibrosis Quística Límite: Humans Idioma: En Revista: Proc Natl Acad Sci U S A Año: 2022 Tipo del documento: Article