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Longitudinal Analysis of PUL 2.0 Domains in Ambulant and Non-Ambulant Duchenne Muscular Dystrophy Patients: How do they Change in Relation to Functional Ability?
Pane, Marika; Coratti, Giorgia; Brogna, Claudia; Bovis, Francesca; D'Amico, Adele; Pegoraro, Elena; Bello, Luca; Sansone, Valeria; Albamonte, Emilio; Ferraroli, Elisabetta; Mazzone, Elena Stacy; Fanelli, Lavinia; Messina, Sonia; Catteruccia, Michela; Cicala, Gianpaolo; Ricci, Martina; Frosini, Silvia; De Luca, Giacomo; Rolle, Enrica; De Sanctis, Roberto; Forcina, Nicola; Norcia, Giulia; Passamano, Luigia; Gardani, Alice; Pini, Antonella; Monaco, Giulia; D'Angelo, Maria Grazia; Capasso, Anna; Leone, Daniela; Zanin, Riccardo; Vita, Gian Luca; Panicucci, Chiara; Bruno, Claudio; Mongini, Tiziana; Ricci, Federica; Berardinelli, Angela; Battini, Roberta; Masson, Riccardo; Baranello, Giovanni; Dosi, Claudia; Bertini, Enrico; Politano, Luisa; Mercuri, Eugenio.
Afiliación
  • Pane M; Pediatric Neurology, Università Cattolica delSacro Cuore, Rome, Italy.
  • Coratti G; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • Brogna C; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • Bovis F; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • D'Amico A; Department of Health Sciences (DISSAL), University of Genova, Genova, Italy.
  • Pegoraro E; Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children'sHospital, Rome, Italy.
  • Bello L; Department of Neurosciences, University of Padua, Padua, Italy.
  • Sansone V; Department of Neurosciences, University of Padua, Padua, Italy.
  • Albamonte E; The NEMO Clinical Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Milan, Italy.
  • Ferraroli E; The NEMO Clinical Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Milan, Italy.
  • Mazzone ES; Pediatric Neurology, Università Cattolica delSacro Cuore, Rome, Italy.
  • Fanelli L; Pediatric Neurology, Università Cattolica delSacro Cuore, Rome, Italy.
  • Messina S; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • Catteruccia M; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
  • Cicala G; Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children'sHospital, Rome, Italy.
  • Ricci M; Pediatric Neurology, Università Cattolica delSacro Cuore, Rome, Italy.
  • Frosini S; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • De Luca G; Pediatric Neurology, Università Cattolica delSacro Cuore, Rome, Italy.
  • Rolle E; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • De Sanctis R; Department of Developmental Neuroscience, IRCCS Stella Maris, Pisa, Italy.
  • Forcina N; Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children'sHospital, Rome, Italy.
  • Norcia G; Neuromuscular Center, AOU Città della Salute e della Scienza, University of Torino, Turin, Italy.
  • Passamano L; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • Gardani A; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • Pini A; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • Monaco G; Department of Experimental Medicine, Cardiomiology and Medical Genetics, Second University of Naples, Naples, Italy.
  • D'Angelo MG; Child and Adolescence NeurologicalUnit, National Neurological Institute Casimiro MondinoFoundation, IRCCS, Pavia, Italy.
  • Capasso A; Child Neurologyand Psychiatry Unit, IRCCS Institute of Neurological Sciences, Bellaria Hospital, Bologna, Italy.
  • Leone D; Child Neurologyand Psychiatry Unit, IRCCS Institute of Neurological Sciences, Bellaria Hospital, Bologna, Italy.
  • Zanin R; Neuro Muscular Unit IRCCS Eugenio Medea, Bosisio Parini, Italy.
  • Vita GL; Pediatric Neurology, Università Cattolica delSacro Cuore, Rome, Italy.
  • Panicucci C; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • Bruno C; Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
  • Mongini T; Developmental Neurology Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy.
  • Ricci F; Unit of Neurology, IRCCS Centro Neurolesi Bonino-Pulejo - P.O. Piemonte, Messina, Italy.
  • Berardinelli A; Center of Translational and Experimental Myology, IRCCS Istituto Giannina Gaslini, and Department of Neuroscience, Rehabilitation, Ophtalmology, Genetics, Maternal and ChildHealth-DINOGMI, University of Genova, Genova, Italy.
  • Battini R; Center of Translational and Experimental Myology, IRCCS Istituto Giannina Gaslini, and Department of Neuroscience, Rehabilitation, Ophtalmology, Genetics, Maternal and ChildHealth-DINOGMI, University of Genova, Genova, Italy.
  • Masson R; Neuromuscular Center, AOU Città della Salute e della Scienza, University of Torino, Turin, Italy.
  • Baranello G; Neuromuscular Center, AOU Città della Salute e della Scienza, University of Torino, Turin, Italy.
  • Dosi C; Child and Adolescence NeurologicalUnit, National Neurological Institute Casimiro MondinoFoundation, IRCCS, Pavia, Italy.
  • Bertini E; Department of Developmental Neuroscience, IRCCS Stella Maris, Pisa, Italy.
  • Politano L; Department of Clinical and Experimental Medicine, University of Pisa, Italy.
  • Mercuri E; Developmental Neurology Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy.
J Neuromuscul Dis ; 10(4): 567-574, 2023.
Article en En | MEDLINE | ID: mdl-37066919

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Distrofia Muscular de Duchenne Límite: Humans Idioma: En Revista: J Neuromuscul Dis Año: 2023 Tipo del documento: Article País de afiliación: Italia

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Distrofia Muscular de Duchenne Límite: Humans Idioma: En Revista: J Neuromuscul Dis Año: 2023 Tipo del documento: Article País de afiliación: Italia