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High-Content Small Molecule Screen Identifies a Novel Compound That Restores AP-4-Dependent Protein Trafficking in Neuronal Models of AP-4-Associated Hereditary Spastic Paraplegia.
Saffari, Afshin; Brechmann, Barbara; Boeger, Cedric; Saber, Wardiya Afshar; Jumo, Hellen; Whye, Dosh; Wood, Delaney; Wahlster, Lara; Alecu, Julian; Ziegler, Marvin; Scheffold, Marlene; Winden, Kellen; Hubbs, Jed; Buttermore, Elizabeth; Barrett, Lee; Borner, Georg; Davies, Alexandra; Sahin, Mustafa; Ebrahimi-Fakhari, Darius.
Afiliación
  • Saffari A; Boston Children's Hospital, Harvard Medical School.
  • Brechmann B; Boston Children's Hospital, Harvard Medical School.
  • Boeger C; Boston Children's Hospital, Harvard Medical School.
  • Saber WA; Boston Children's Hospital/Harvard Medical School.
  • Whye D; Boston Children's Hospital, Harvard Medical School.
  • Wood D; Boston Children's Hospital, Harvard Medical School.
  • Wahlster L; Boston Children's Hospital, Harvard Medical School.
  • Alecu J; Boston Children's Hospital, Harvard Medical School.
  • Ziegler M; Harvard Medical School.
  • Scheffold M; Boston Children's Hospital, Harvard Medical School.
  • Winden K; Boston Children's Hospital.
  • Hubbs J; Boston Children's Hospital.
  • Buttermore E; Boston Children's Hospital.
  • Barrett L; Boston Children's Hospital.
  • Borner G; Max Planck Institute of Biochemistry.
  • Davies A; Max Planck Institute of Biochemistry.
  • Sahin M; Boston Children's Hospital.
  • Ebrahimi-Fakhari D; Boston Children's Hospital, Harvard Medical School.
Res Sq ; 2023 Jun 12.
Article en En | MEDLINE | ID: mdl-37398196

Texto completo: 1 Base de datos: MEDLINE Tipo de estudio: Risk_factors_studies Idioma: En Revista: Res Sq Año: 2023 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Tipo de estudio: Risk_factors_studies Idioma: En Revista: Res Sq Año: 2023 Tipo del documento: Article