Your browser doesn't support javascript.
loading
Highly Efficient Ex Vivo Correction of COL7A1 through Ribonucleoprotein-Based CRISPR/Cas9 and Homology-Directed Repair to Treat Recessive Dystrophic Epidermolysis Bullosa.
Berthault, Camille; Gaucher, Sonia; Gouin, Olivier; Schmitt, Alain; Chen, Mei; Woodley, David; Titeux, Matthias; Hovnanian, Alain; Izmiryan, Araksya.
Afiliación
  • Berthault C; INSERM UMR 1163, Laboratory of Genetic skin diseases, Imagine Institute, Paris, France; Paris Cité University, Paris, France.
  • Gaucher S; INSERM UMR 1163, Laboratory of Genetic skin diseases, Imagine Institute, Paris, France; Paris Cité University, Paris, France.
  • Gouin O; INSERM UMR 1163, Laboratory of Genetic skin diseases, Imagine Institute, Paris, France; Paris Cité University, Paris, France.
  • Schmitt A; Electronic Microscopy Facility, INSERM UMR 1016, Cochin Institute, Paris, France.
  • Chen M; Department of Dermatology, Keck School of Medicine, University of Southern California, Los Angeles, California, USA.
  • Woodley D; Department of Dermatology, Keck School of Medicine, University of Southern California, Los Angeles, California, USA; Norris Comprehensive Cancer Center, Keck School of Medicine, University of Southern California, Los Angeles, California, USA.
  • Titeux M; INSERM UMR 1163, Laboratory of Genetic skin diseases, Imagine Institute, Paris, France; Paris Cité University, Paris, France.
  • Hovnanian A; INSERM UMR 1163, Laboratory of Genetic skin diseases, Imagine Institute, Paris, France; Paris Cité University, Paris, France; Department of Genomic Medicine for Rare Diseases, Necker Hospital for Sick Children, Assistance Publique-Hôpitaux de Paris (APHP), Paris, France.
  • Izmiryan A; INSERM UMR 1163, Laboratory of Genetic skin diseases, Imagine Institute, Paris, France; Paris Cité University, Paris, France. Electronic address: araksya.izmiryan@inserm.fr.
J Invest Dermatol ; 2023 Dec 01.
Article en En | MEDLINE | ID: mdl-38043638

Texto completo: 1 Base de datos: MEDLINE Idioma: En Revista: J Invest Dermatol Año: 2023 Tipo del documento: Article País de afiliación: Francia

Texto completo: 1 Base de datos: MEDLINE Idioma: En Revista: J Invest Dermatol Año: 2023 Tipo del documento: Article País de afiliación: Francia