Detalhe da pesquisa
1.
Targeted replacement of full-length CFTR in human airway stem cells by CRISPR-Cas9 for pan-mutation correction in the endogenous locus.
Mol Ther
; 30(1): 223-237, 2022 01 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-33794364
2.
GPR108 Is a Highly Conserved AAV Entry Factor.
Mol Ther
; 28(2): 367-381, 2020 02 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-31784416
3.
Differential role for phosphorylation in alternative polyadenylation function versus nuclear import of SR-like protein CPSF6.
Nucleic Acids Res
; 47(9): 4663-4683, 2019 05 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-30916345
4.
An Alternate Route for Adeno-associated Virus (AAV) Entry Independent of AAV Receptor.
J Virol
; 92(7)2018 04 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-29343568
5.
AAV6 Is Superior to Clade F AAVs in Stimulating Homologous Recombination-Based Genome Editing in Human HSPCs.
Mol Ther
; 27(10): 1701-1705, 2019 10 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-31537456
6.
Reply to "Efficient Nuclease-free HR by Clade F AAV Requires High MOIs with High Quality Vectors".
Mol Ther
; 27(12): 2063, 2019 12 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-31735604
7.
A simultaneous knockout knockin genome editing strategy in HSPCs potently inhibits CCR5- and CXCR4-tropic HIV-1 infection.
Cell Stem Cell
; 31(4): 499-518.e6, 2024 Apr 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-38579682
8.
Transient inhibition of 53BP1 increases the frequency of targeted integration in human hematopoietic stem and progenitor cells.
Nat Commun
; 15(1): 111, 2024 Jan 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-38169468
9.
Combining Cell-Intrinsic and -Extrinsic Resistance to HIV-1 By Engineering Hematopoietic Stem Cells for CCR5 Knockout and B Cell Secretion of Therapeutic Antibodies.
bioRxiv
; 2024 Mar 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-38496600
10.
High-efficiency transgene integration by homology-directed repair in human primary cells using DNA-PKcs inhibition.
Nat Biotechnol
; 2023 Aug 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-37537500