Detalhe da pesquisa
1.
High resolution time-course mapping of early transcriptomic, molecular and cellular phenotypes in Huntington's disease CAG knock-in mice across multiple genetic backgrounds.
Hum Mol Genet
; 26(5): 913-922, 2017 03 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-28334820
2.
Transcriptional regulatory networks underlying gene expression changes in Huntington's disease.
Mol Syst Biol
; 14(3): e7435, 2018 03 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-29581148
3.
Translating dosage compensation to trisomy 21.
Nature
; 500(7462): 296-300, 2013 Aug 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-23863942
4.
Site-specific genome editing in Plasmodium falciparum using engineered zinc-finger nucleases.
Nat Methods
; 9(10): 993-8, 2012 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-22922501
5.
Activation domains for controlling plant gene expression using designed transcription factors.
Plant Biotechnol J
; 11(6): 671-80, 2013 Aug.
Artigo
em Inglês
| MEDLINE | ID: mdl-23521778
6.
Genome-Scale Transcriptional Regulatory Network Models of Psychiatric and Neurodegenerative Disorders.
Cell Syst
; 8(2): 122-135.e7, 2019 02 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-30772379
7.
Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington's disease.
Nat Med
; 25(7): 1131-1142, 2019 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-31263285
8.
Enhanced retinal responses in Huntington's disease patients.
J Huntingtons Dis
; 6(3): 237-247, 2017.
Artigo
em Inglês
| MEDLINE | ID: mdl-28968243
9.
Targeted gene addition in human CD34(+) hematopoietic cells for correction of X-linked chronic granulomatous disease.
Nat Biotechnol
; 34(4): 424-9, 2016 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-26950749