Detalhe da pesquisa
1.
Long-term effect of human mini-dystrophin in transgenic mdx mice improves muscle physiological function.
FASEB J
; 35(6): e21628, 2021 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-33982338
2.
An engineered serum albumin-binding AAV9 capsid achieves improved liver transduction after intravenous delivery in mice.
Gene Ther
; 27(5): 237-244, 2020 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-31819202
3.
Neonatal Systemic AAV-Mediated Gene Delivery of GDF11 Inhibits Skeletal Muscle Growth.
Mol Ther
; 26(4): 1109-1117, 2018 04 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-29503194
4.
Adeno-Associated Virus-Mediated Mini-Agrin Delivery Is Unable to Rescue Disease Phenotype in a Mouse Model of Limb Girdle Muscular Dystrophy Type 2I.
Am J Pathol
; 187(2): 431-440, 2017 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-28107841
5.
Overcoming Insulin Insufficiency by Forced Follistatin Expression in ß-cells of db/db Mice.
Mol Ther
; 23(5): 866-874, 2015 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-25676679
6.
A practical method for monitoring FRET-based biosensors in living animals using two-photon microscopy.
Am J Physiol Cell Physiol
; 309(11): C724-35, 2015 Dec 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-26333599
7.
Muscle and heart function restoration in a limb girdle muscular dystrophy 2I (LGMD2I) mouse model by systemic FKRP gene delivery.
Mol Ther
; 22(11): 1890-9, 2014 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-25048216
8.
Adeno-associated virus 9 mediated FKRP gene therapy restores functional glycosylation of α-dystroglycan and improves muscle functions.
Mol Ther
; 21(10): 1832-40, 2013 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-23817215
9.
Enhancing muscle membrane repair by gene delivery of MG53 ameliorates muscular dystrophy and heart failure in δ-Sarcoglycan-deficient hamsters.
Mol Ther
; 20(4): 727-35, 2012 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-22314291
10.
The Integrated Bioinformatic Assay of Genetic Expression Features and Analyses of Traditional Chinese Medicine Specific Constitution Reveal Metabolic Characteristics and Targets in Steatosis of Nonalcoholic Fatty Liver Disease.
Hepat Med
; 15: 165-183, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37822344
11.
Post-Natal knockdown of fukutin-related protein expression in muscle by long-termRNA interference induces dystrophic pathology [corrected].
Am J Pathol
; 178(1): 261-72, 2011 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-21224063
12.
A myocardium tropic adeno-associated virus (AAV) evolved by DNA shuffling and in vivo selection.
Proc Natl Acad Sci U S A
; 106(10): 3946-51, 2009 Mar 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-19234115
13.
Widespread muscle expression of an AAV9 human mini-dystrophin vector after intravenous injection in neonatal dystrophin-deficient dogs.
Mol Ther
; 18(8): 1501-8, 2010 Aug.
Artigo
em Inglês
| MEDLINE | ID: mdl-20517298
14.
Gene therapy using an ortholog of human fragile X mental retardation protein partially rescues behavioral abnormalities and EEG activity.
Mol Ther Methods Clin Dev
; 22: 196-209, 2021 Sep 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-34485605
15.
A GDF11/myostatin inhibitor, GDF11 propeptide-Fc, increases skeletal muscle mass and improves muscle strength in dystrophic mdx mice.
Skelet Muscle
; 9(1): 16, 2019 05 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-31133057
16.
Myostatin propeptide gene delivery by adeno-associated virus serotype 8 vectors enhances muscle growth and ameliorates dystrophic phenotypes in mdx mice.
Hum Gene Ther
; 19(3): 241-54, 2008 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-18288893
17.
Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart.
Nat Biotechnol
; 23(3): 321-8, 2005 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-15735640
18.
MicroRNA-206 Downregulation Improves Therapeutic Gene Expression and Motor Function in mdx Mice.
Mol Ther Nucleic Acids
; 12: 283-293, 2018 Sep 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30195767
19.
Amelioration of Muscle and Nerve Pathology in LAMA2 Muscular Dystrophy by AAV9-Mini-Agrin.
Mol Ther Methods Clin Dev
; 9: 47-56, 2018 Jun 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-29766020
20.
Follistatin N terminus differentially regulates muscle size and fat in vivo.
Exp Mol Med
; 49(9): e377, 2017 09 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-28912572