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Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector.
Choudhury, Sourav R; Harris, Anne F; Cabral, Damien J; Keeler, Allison M; Sapp, Ellen; Ferreira, Jennifer S; Gray-Edwards, Heather L; Johnson, Jacob A; Johnson, Aime K; Su, Qin; Stoica, Lorelei; DiFiglia, Marian; Aronin, Neil; Martin, Douglas R; Gao, Guangping; Sena-Esteves, Miguel.
Afiliação
  • Choudhury SR; Department of Neurology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Harris AF; Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Cabral DJ; Department of Neurology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Keeler AM; Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Sapp E; Department of Neurology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Ferreira JS; Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Gray-Edwards HL; Department of Neurology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Johnson JA; Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Johnson AK; Department of Neurology, Massachusetts General Hospital, Charlestown, Massachusetts, USA.
  • Su Q; Department of Neurology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Stoica L; Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • DiFiglia M; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, Alabama, USA.
  • Aronin N; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, Alabama, USA.
  • Martin DR; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, Alabama, USA.
  • Gao G; Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Sena-Esteves M; Department of Microbiology & Physiological Systems, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
Mol Ther ; 24(4): 726-35, 2016 Apr.
Article em En | MEDLINE | ID: mdl-26708003

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Peptídeos / Transdução Genética / Sistema Nervoso Central / Proteínas do Capsídeo Idioma: En Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Peptídeos / Transdução Genética / Sistema Nervoso Central / Proteínas do Capsídeo Idioma: En Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Estados Unidos