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Innovative Curative Treatment of Beta Thalassemia: Cost-Efficacy Analysis of Gene Therapy Versus Allogenic Hematopoietic Stem-Cell Transplantation.
Coquerelle, Séverine; Ghardallou, Mariem; Rais, Setti; Taupin, Pierre; Touzot, Fabien; Boquet, Laure; Blanche, Stéphane; Benaouadi, Semir; Brice, Thomas; Tuchmann-Durand, Caroline; Ribeil, Jean Antoine; Magrin, Elisa; Lissillour, Etienne; Rochaix, Lise; Cavazzana, Marina; Durand-Zaleski, Isabelle.
Afiliação
  • Coquerelle S; 1 URC Eco, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Ghardallou M; 2 Université Paris Diderot, Sorbonne Paris Cité, France.
  • Rais S; 3 CRESS, INSERM UMR 1153, Paris, France.
  • Taupin P; 1 URC Eco, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Touzot F; 4 Hospinnomics (Paris School of Economics, Assistance Publique-Hôpitaux de Paris), Paris, France.
  • Boquet L; 5 Institut Imagine, Paris, France.
  • Blanche S; 6 Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Benaouadi S; 6 Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Brice T; 7 Département de Pédiatrie - Centre de Recherche du CHU Sainte-Justine, Montréal, Canada.
  • Tuchmann-Durand C; 5 Institut Imagine, Paris, France.
  • Ribeil JA; 6 Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Magrin E; 6 Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Lissillour E; 6 Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Rochaix L; 5 Institut Imagine, Paris, France.
  • Cavazzana M; 6 Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Durand-Zaleski I; 5 Institut Imagine, Paris, France.
Hum Gene Ther ; 30(6): 753-761, 2019 06.
Article em En | MEDLINE | ID: mdl-30700149

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Talassemia beta / Transplante de Células-Tronco Hematopoéticas Idioma: En Ano de publicação: 2019 Tipo de documento: Article País de afiliação: França

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Talassemia beta / Transplante de Células-Tronco Hematopoéticas Idioma: En Ano de publicação: 2019 Tipo de documento: Article País de afiliação: França