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Polyglutamine Ataxias: Our Current Molecular Understanding and What the Future Holds for Antisense Therapies.
McIntosh, Craig S; Li, Dunhui; Wilton, Steve D; Aung-Htut, May T.
Afiliação
  • McIntosh CS; Molecular Therapy Laboratory, Centre for Molecular Medicine and Innovative Therapeutics, Health Futures Institute Murdoch University, Discovery Way, Murdoch, WA 6150, Australia.
  • Li D; Perron Institute for Neurological and Translational Science, Centre for Neuromuscular and Neurological Disorders, The University of Western Australia, Nedlands, WA 6009, Australia.
  • Wilton SD; Molecular Therapy Laboratory, Centre for Molecular Medicine and Innovative Therapeutics, Health Futures Institute Murdoch University, Discovery Way, Murdoch, WA 6150, Australia.
  • Aung-Htut MT; Perron Institute for Neurological and Translational Science, Centre for Neuromuscular and Neurological Disorders, The University of Western Australia, Nedlands, WA 6009, Australia.
Biomedicines ; 9(11)2021 Oct 20.
Article em En | MEDLINE | ID: mdl-34829728

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Austrália

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Austrália