Detalhe da pesquisa
1.
Titin M-line insertion sequence 7 is required for proper cardiac function in mice.
J Cell Sci
; 134(18)2021 09 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-34401916
2.
Integrated time-lapse and single-cell transcription studies highlight the variable and dynamic nature of human hematopoietic cell fate commitment.
PLoS Biol
; 15(7): e2001867, 2017 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-28749943
3.
Single-Cell-Based Analysis Highlights a Surge in Cell-to-Cell Molecular Variability Preceding Irreversible Commitment in a Differentiation Process.
PLoS Biol
; 14(12): e1002585, 2016 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-28027290
4.
Peptides derived from evolutionarily conserved domains in Beclin-1 and Beclin-2 enhance the entry of lentiviral vectors into human cells.
J Biol Chem
; 292(45): 18672-18681, 2017 11 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-28928217
5.
Serum proteomic profiling reveals fragments of MYOM3 as potential biomarkers for monitoring the outcome of therapeutic interventions in muscular dystrophies.
Hum Mol Genet
; 24(17): 4916-32, 2015 Sep 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-26060189
6.
Combination of imaging flow cytometry and time-lapse microscopy for the study of label-free morphology dynamics of hematopoietic cells.
Cytometry A
; 91(3): 254-260, 2017 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-28248454
7.
Inhibition of the myostatin/Smad signaling pathway by short decorin-derived peptides.
Exp Cell Res
; 341(2): 187-95, 2016 Feb 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-26844629
8.
Mouse models of primary central nervous system lymphomas: tools for basing funding and therapeutic strategies.
J Neurooncol
; 121(1): 9-18, 2015 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-25300908
9.
A functional mini-GDE transgene corrects impairment in models of glycogen storage disease type III.
J Clin Invest
; 134(2)2024 Jan 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-38015640
10.
Synergism of dual AAV gene therapy and rapamycin rescues GSDIII phenotype in muscle and liver.
JCI Insight
; 2024 May 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-38753465
11.
Pathological modeling of glycogen storage disease type III with CRISPR/Cas9 edited human pluripotent stem cells.
Front Cell Dev Biol
; 11: 1163427, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37250895
12.
Artificial intelligence workflow quantifying muscle features on Hematoxylin-Eosin stained sections reveals dystrophic phenotype amelioration upon treatment.
Sci Rep
; 12(1): 19913, 2022 11 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-36402802
13.
Characterization of Neuromuscular Junctions in Mice by Combined Confocal and Super-Resolution Microscopy.
J Vis Exp
; (178)2021 12 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-34958074
14.
Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates.
Nat Commun
; 12(1): 6393, 2021 11 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-34737297
15.
An AAV-SGCG Dose-Response Study in a γ-Sarcoglycanopathy Mouse Model in the Context of Mechanical Stress.
Mol Ther Methods Clin Dev
; 13: 494-502, 2019 Jun 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-31194043
16.
Temporary Reduction of Membrane CD4 with the Antioxidant MnTBAP Is Sufficient to Prevent Immune Responses Induced by Gene Transfer.
Mol Ther Methods Clin Dev
; 14: 285-299, 2019 Sep 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-31497619
17.
Vectofusin-1, a potent peptidic enhancer of viral gene transfer forms pH-dependent α-helical nanofibrils, concentrating viral particles.
Acta Biomater
; 64: 259-268, 2017 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-29017974
18.
Bioluminescence-Based Tumor Quantification Method for Monitoring Tumor Progression and Treatment Effects in Mouse Lymphoma Models.
J Vis Exp
; (113)2016 07 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-27501019
19.
Single Cell Dynamics Causes Pareto-Like Effect in Stimulated T Cell Populations.
Sci Rep
; 5: 17756, 2015 Dec 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-26648396
20.
Lymphoma B-cell responsiveness to CpG-DNA depends on the tumor microenvironment.
J Exp Clin Cancer Res
; 32: 18, 2013 Apr 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-23561041