Detalhe da pesquisa
1.
Mitapivat versus Placebo for Pyruvate Kinase Deficiency.
N Engl J Med
; 386(15): 1432-1442, 2022 04 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-35417638
2.
A randomized clinical trial of the efficacy and safety of rivipansel for sickle cell vaso-occlusive crisis.
Blood
; 141(2): 168-179, 2023 01 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-35981565
3.
Birth Prevalence of Sickle Cell Disease and County-Level Social Vulnerability - Sickle Cell Data Collection Program, 11 States, 2016-2020.
MMWR Morb Mortal Wkly Rep
; 73(12): 248-254, 2024 Mar 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-38547025
4.
Treatment of relapsed/refractory severe aplastic anemia in children: Evidence-based recommendations.
Pediatr Blood Cancer
; : e31075, 2024 May 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-38764170
5.
Treatment of newly diagnosed severe aplastic anemia in children: Evidence-based recommendations.
Pediatr Blood Cancer
; : e31070, 2024 May 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-38757488
6.
The pyruvate kinase (PK) to hexokinase enzyme activity ratio and erythrocyte PK protein level in the diagnosis and phenotype of PK deficiency.
Br J Haematol
; 192(6): 1092-1096, 2021 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-32463523
7.
Diagnostic work-up for severe aplastic anemia in children: Consensus of the North American Pediatric Aplastic Anemia Consortium.
Am J Hematol
; 96(11): 1491-1504, 2021 11 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-34342889
8.
Pyruvate kinase deficiency in children.
Pediatr Blood Cancer
; 68(9): e29148, 2021 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-34125488
9.
Clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study.
Blood
; 131(20): 2183-2192, 2018 05 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-29549173
10.
How I approach hereditary hemolytic anemia and splenectomy.
Pediatr Blood Cancer
; 67(11): e28337, 2020 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-32391969
11.
LONG-TERM HEMATOLOGIC AND CLINICAL OUTCOMES OF SPLENECTOMY IN CHILDREN WITH HEREDITARY SPHEROCYTOSIS AND SICKLE CELL DISEASE.
Pediatr Blood Cancer
; 67(8)2020 Aug.
Artigo
em Inglês
| MEDLINE | ID: mdl-37132000
12.
Immunosuppressive therapy for pediatric aplastic anemia: a North American Pediatric Aplastic Anemia Consortium study.
Haematologica
; 104(10): 1974-1983, 2019 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30948484
13.
Second-line treatments in children with immune thrombocytopenia: Effect on platelet count and patient-centered outcomes.
Am J Hematol
; 94(7): 741-750, 2019 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30945320
14.
Physician decision making in selection of second-line treatments in immune thrombocytopenia in children.
Am J Hematol
; 93(7): 882-888, 2018 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-29659042
15.
Bleeding and thrombotic complications of pediatric liver transplant.
Pediatr Blood Cancer
; 65(5): e26955, 2018 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-29350493
16.
Hydroxycarbamide versus chronic transfusion for maintenance of transcranial doppler flow velocities in children with sickle cell anaemia-TCD With Transfusions Changing to Hydroxyurea (TWiTCH): a multicentre, open-label, phase 3, non-inferiority trial.
Lancet
; 387(10019): 661-670, 2016 Feb 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-26670617
17.
SARS-CoV-2 vaccination in pediatric patients with immune thrombocytopenia.
Pediatr Blood Cancer
; 69(7): e29760, 2022 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-35561101
18.
The clinical severity of hemoglobin S/Black (A γδß)0 -thalassemia.
Pediatr Blood Cancer
; 64(11)2017 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-28453928
19.
Effects of hydroxyurea treatment for patients with hemoglobin SC disease.
Am J Hematol
; 91(2): 238-42, 2016 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-26615793
20.
Characterization of the severe phenotype of pyruvate kinase deficiency.
Am J Hematol
; 95(10): E281-E285, 2020 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-32619047