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Systematic neonatal screening for severe combined immunodeficiency and severe T-cell lymphopenia: Analysis of cost-effectiveness based on French real field data.
Clément, Marie Caroline; Mahlaoui, Nizar; Mignot, Cécile; Le Bihan, Christine; Rabetrano, Hasina; Hoang, Ly; Neven, Bénédicte; Moshous, Despina; Cavazzana, Marina; Blanche, Stéphane; Fischer, Alain; Audrain, Marie; Durand-Zaleski, Isabelle.
Affiliation
  • Clément MC; URC Eco (Clinical Research Unit in Health Economics), Assistance Publique-Hôpitaux de Paris, Hôtel Dieu Hospital, Paris, France.
  • Mahlaoui N; Pediatric Hematology-Immunology and Rheumatology Unit, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France; CEREDIH (French National Reference Center for Primary Immune Deficiencies), Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades Universit
  • Mignot C; CEREDIH (French National Reference Center for Primary Immune Deficiencies), Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.
  • Le Bihan C; Medical information unit, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.
  • Rabetrano H; URC Eco (Clinical Research Unit in Health Economics), Assistance Publique-Hôpitaux de Paris, Hôtel Dieu Hospital, Paris, France.
  • Hoang L; URC Eco (Clinical Research Unit in Health Economics), Assistance Publique-Hôpitaux de Paris, Hôtel Dieu Hospital, Paris, France.
  • Neven B; Pediatric Hematology-Immunology and Rheumatology Unit, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France; CEREDIH (French National Reference Center for Primary Immune Deficiencies), Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades Universit
  • Moshous D; Pediatric Hematology-Immunology and Rheumatology Unit, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France; CEREDIH (French National Reference Center for Primary Immune Deficiencies), Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades Universit
  • Cavazzana M; Paris Descartes University, Sorbonne Paris Cité, Imagine Institute, Paris, France; Biotherapy Department, Necker Children's University Hospital, AP-HP, Paris, France; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, AP-HP, INSERM, Paris, France.
  • Blanche S; Pediatric Hematology-Immunology and Rheumatology Unit, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France; CEREDIH (French National Reference Center for Primary Immune Deficiencies), Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades Universit
  • Fischer A; Pediatric Hematology-Immunology and Rheumatology Unit, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France; CEREDIH (French National Reference Center for Primary Immune Deficiencies), Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades Universit
  • Audrain M; Immunology Laboratory, Nantes University Hospital, Nantes, France.
  • Durand-Zaleski I; URC Eco (Clinical Research Unit in Health Economics), Assistance Publique-Hôpitaux de Paris, Hôtel Dieu Hospital, Paris, France; Public Health Unit, Henri Mondor Hospital, Assistance Publique-Hôpitaux de Paris, INSERM UMR 1123, Créteil, France. Electronic address: isabelle.durand-zaleski@hmn.aphp.fr
J Allergy Clin Immunol ; 135(6): 1589-93, 2015 Jun.
Article in En | MEDLINE | ID: mdl-25840725

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Biological Assay / Neonatal Screening / Severe Combined Immunodeficiency / Cost-Benefit Analysis / Hematopoietic Stem Cell Transplantation / Lymphopenia Type of study: Diagnostic_studies / Health_economic_evaluation / Screening_studies Limits: Female / Humans / Infant / Male / Newborn Country/Region as subject: Europa Language: En Journal: J Allergy Clin Immunol Year: 2015 Type: Article Affiliation country: France

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Biological Assay / Neonatal Screening / Severe Combined Immunodeficiency / Cost-Benefit Analysis / Hematopoietic Stem Cell Transplantation / Lymphopenia Type of study: Diagnostic_studies / Health_economic_evaluation / Screening_studies Limits: Female / Humans / Infant / Male / Newborn Country/Region as subject: Europa Language: En Journal: J Allergy Clin Immunol Year: 2015 Type: Article Affiliation country: France