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Long-Term Effects of Gene Therapy in a Novel Mouse Model of Human MFRP-Associated Retinopathy.
Chekuri, Anil; Sahu, Bhubanananda; Chavali, Venkata Ramana Murthy; Voronchikhina, Marina; Soto-Hermida, Angel; Suk, John J; Alapati, Akhila N; Bartsch, Dirk-Uwe; Ayala-Ramirez, Raul; Zenteno, Juan C; Dinculescu, Astra; Jablonski, Monica M; Borooah, Shyamanga; Ayyagari, Radha.
Affiliation
  • Chekuri A; 1 Shiley Eye Institute, University of California San Diego, La Jolla, California.
  • Sahu B; 1 Shiley Eye Institute, University of California San Diego, La Jolla, California.
  • Chavali VRM; 2 Department of Ophthalmology and Visual sciences, Kentucky Lions Eye Center, University of Louisville, Louisville, Kentucky.
  • Voronchikhina M; 1 Shiley Eye Institute, University of California San Diego, La Jolla, California.
  • Soto-Hermida A; 3 Scheie Eye Institute, Department of Ophthalmology, University of Pennsylvania, Philadelphia, Pennsylvania.
  • Suk JJ; 1 Shiley Eye Institute, University of California San Diego, La Jolla, California.
  • Alapati AN; 1 Shiley Eye Institute, University of California San Diego, La Jolla, California.
  • Bartsch DU; 1 Shiley Eye Institute, University of California San Diego, La Jolla, California.
  • Ayala-Ramirez R; 1 Shiley Eye Institute, University of California San Diego, La Jolla, California.
  • Zenteno JC; 1 Shiley Eye Institute, University of California San Diego, La Jolla, California.
  • Dinculescu A; 4 Department of Genetics-Research Unit, Institute of Ophthalmology, Conde de Valenciana, Mexico City, Mexico.
  • Jablonski MM; 4 Department of Genetics-Research Unit, Institute of Ophthalmology, Conde de Valenciana, Mexico City, Mexico.
  • Borooah S; 5 Department of Biochemistry, Faculty of Medicine, UNAM, Mexico City, Mexico.
  • Ayyagari R; 6 Department of Ophthalmology, College of Medicine, University of Florida, Gainesville, Florida.
Hum Gene Ther ; 30(5): 632-650, 2019 05.
Article in En | MEDLINE | ID: mdl-30499344

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Retinal Diseases / Genetic Therapy / Genetic Predisposition to Disease / Membrane Proteins Type of study: Diagnostic_studies / Prognostic_studies / Risk_factors_studies Limits: Animals / Humans Language: En Journal: Hum Gene Ther Journal subject: GENETICA MEDICA / TERAPEUTICA Year: 2019 Type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Retinal Diseases / Genetic Therapy / Genetic Predisposition to Disease / Membrane Proteins Type of study: Diagnostic_studies / Prognostic_studies / Risk_factors_studies Limits: Animals / Humans Language: En Journal: Hum Gene Ther Journal subject: GENETICA MEDICA / TERAPEUTICA Year: 2019 Type: Article