Thrombotic Microangiopathy Following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series.
J Pediatr
; 231: 265-268, 2021 04.
Article
in En
| MEDLINE
| ID: mdl-33259859
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Biological Products
/
Recombinant Fusion Proteins
/
Muscular Atrophy, Spinal
/
Thrombotic Microangiopathies
Type of study:
Prognostic_studies
Limits:
Female
/
Humans
/
Infant
Language:
En
Journal:
J Pediatr
Year:
2021
Type:
Article