Durable vision improvement after a single treatment with antisense oligonucleotide sepofarsen: a case report.
Nat Med
; 27(5): 785-789, 2021 05.
Article
in En
| MEDLINE
| ID: mdl-33795869
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Genetic Therapy
/
Oligonucleotides, Antisense
/
Cell Cycle Proteins
/
Cytoskeletal Proteins
/
Leber Congenital Amaurosis
/
Ciliopathies
/
Antigens, Neoplasm
Limits:
Humans
Language:
En
Journal:
Nat Med
Journal subject:
BIOLOGIA MOLECULAR
/
MEDICINA
Year:
2021
Type:
Article
Affiliation country:
United States