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Etavopivat, a Pyruvate Kinase Activator in Red Blood Cells, for the Treatment of Sickle Cell Disease.
Schroeder, Patricia; Fulzele, Keertik; Forsyth, Sanjeev; Ribadeneira, Maria D; Guichard, Sylvie; Wilker, Erik; Marshall, C Gary; Drake, Adam; Fessler, Rose; Konstantinidis, Diamantis G; Seu, Katie G; Kalfa, Theodosia A.
Affiliation
  • Schroeder P; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Fulzele K; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Forsyth S; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Ribadeneira MD; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Guichard S; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Wilker E; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Marshall CG; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Drake A; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Fessler R; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Konstantinidis DG; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Seu KG; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
  • Kalfa TA; Forma Therapeutics, Watertown, Massachusetts (P.S., K.F., S.F., M.D.R., S.G.); Tango Therapeutics, Cambridge, Massachusetts (E.W.); Repare Therapeutics, Cambridge, Massachusetts (C.G.M.); Ichnos Sciences, Epalinges, Switzerland (A.D.); Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
J Pharmacol Exp Ther ; 380(3): 210-219, 2022 03.
Article in En | MEDLINE | ID: mdl-35031585

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hemoglobin, Sickle / Anemia, Sickle Cell Limits: Animals / Humans Language: En Journal: J Pharmacol Exp Ther Year: 2022 Type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hemoglobin, Sickle / Anemia, Sickle Cell Limits: Animals / Humans Language: En Journal: J Pharmacol Exp Ther Year: 2022 Type: Article