Long-term multisystemic efficacy of migalastat on Fabry-associated clinical events, including renal, cardiac and cerebrovascular outcomes.
J Med Genet
; 60(7): 722-731, 2023 07.
Article
in En
| MEDLINE
| ID: mdl-36543533
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Fabry Disease
Type of study:
Prognostic_studies
/
Risk_factors_studies
Limits:
Female
/
Humans
Language:
En
Journal:
J Med Genet
Year:
2023
Type:
Article
Affiliation country:
United kingdom