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Evaluation of Cellular Immune Response to Adeno-Associated Virus-Based Gene Therapy.
Gorovits, Boris; Azadeh, Mitra; Buchlis, George; Fiscella, Michele; Harrison, Travis; Havert, Mike; Janetzki, Sylvia; Jawa, Vibha; Long, Brian; Mahnke, Yolanda D; McDermott, Andrew; Milton, Mark; Nelson, Robert; Vettermann, Christian; Wu, Bonnie.
Affiliation
  • Gorovits B; Sana Biotechnology, Cambridge, Massachusetts, USA. boris.gorovits@sana.com.
  • Azadeh M; Ultragenyx Pharmaceutical Inc, Novato, California, USA.
  • Buchlis G; University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Fiscella M; Regenxbio Inc, Rockville, Maryland, USA.
  • Harrison T; Precision for Medicine, Inc, Redwood City, California, USA.
  • Havert M; Gene Therapy Partners, San Diego, California, USA.
  • Janetzki S; ZellNet Consulting, Inc, Fort Lee, New Jersey, USA.
  • Jawa V; Bristol Myers Squibb Pharmaceutical, Princeton, New Jersey, USA.
  • Long B; BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Mahnke YD; FlowKnowHow LLC, Brooklyn, New York, USA.
  • McDermott A; Labcorp Early Development Laboratories Inc, Indianapolis, Indiana, USA.
  • Milton M; Lake Boon Pharmaceutical Consulting LLC, Hudson, New York, USA.
  • Nelson R; BioAgilytix Europe GmbH, Hamburg, Germany.
  • Vettermann C; BioMarin Pharmaceutical Inc, Novato, California, USA.
  • Wu B; Janssen Pharmaceuticals, Raritan, New Jersey, USA.
AAPS J ; 25(3): 47, 2023 04 26.
Article in En | MEDLINE | ID: mdl-37101079

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Dependovirus Type of study: Guideline / Risk_factors_studies Language: En Journal: AAPS J Journal subject: FARMACOLOGIA / TERAPIA POR MEDICAMENTOS Year: 2023 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Dependovirus Type of study: Guideline / Risk_factors_studies Language: En Journal: AAPS J Journal subject: FARMACOLOGIA / TERAPIA POR MEDICAMENTOS Year: 2023 Type: Article Affiliation country: United States