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Enveloped viruses pseudotyped with mammalian myogenic cell fusogens target skeletal muscle for gene delivery.
Hindi, Sajedah M; Petrany, Michael J; Greenfeld, Elena; Focke, Leah C; Cramer, Alyssa A W; Whitt, Michael A; Khairallah, Ramzi J; Ward, Christopher W; Chamberlain, Jeffrey S; Podbilewicz, Benjamin; Prasad, Vikram; Millay, Douglas P.
Afiliación
  • Hindi SM; Division of Molecular Cardiovascular Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Petrany MJ; Division of Molecular Cardiovascular Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Greenfeld E; Department of Biology, Technion-Israel Institute of Technology, Haifa, Israel.
  • Focke LC; Division of Molecular Cardiovascular Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Cramer AAW; Division of Molecular Cardiovascular Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Whitt MA; Department of Microbiology, Immunology, and Biochemistry, University of Tennessee Health Science Center, Memphis, TN, USA.
  • Khairallah RJ; Myologica, LLC, New Market, MD, USA.
  • Ward CW; Department of Orthopedics and Center for Biomedical Engineering and Technology (BioMET), University of Maryland School of Medicine, Baltimore, MD, USA.
  • Chamberlain JS; Departments of Neurology, Medicine and Biochemistry, Wellstone Muscular Dystrophy Specialized Research Center, University of Washington School of Medicine, Seattle, WA, USA.
  • Podbilewicz B; Department of Biology, Technion-Israel Institute of Technology, Haifa, Israel.
  • Prasad V; Division of Molecular Cardiovascular Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Millay DP; Division of Molecular Cardiovascular Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH, USA. Electronic address: douglas.millay@cchmc.org.
Cell ; 186(10): 2062-2077.e17, 2023 05 11.
Article en En | MEDLINE | ID: mdl-37075755

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Lentivirus / Músculo Esquelético / Distrofia Muscular de Duchenne / Bioingeniería / Proteínas de la Membrana Límite: Animals Idioma: En Revista: Cell Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Lentivirus / Músculo Esquelético / Distrofia Muscular de Duchenne / Bioingeniería / Proteínas de la Membrana Límite: Animals Idioma: En Revista: Cell Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos