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Treatment effect of idebenone on inspiratory function in patients with Duchenne muscular dystrophy.
Buyse, Gunnar M; Voit, Thomas; Schara, Ulrike; Straathof, Chiara S M; D'Angelo, Maria Grazia; Bernert, Günther; Cuisset, Jean-Marie; Finkel, Richard S; Goemans, Nathalie; Rummey, Christian; Leinonen, Mika; Mayer, Oscar H; Spagnolo, Paolo; Meier, Thomas; McDonald, Craig M.
Afiliação
  • Buyse GM; University Hospitals Leuven, Leuven, Belgium.
  • Voit T; Institut de Myologie, UPMC INSERM UMR 974, CNRS FRE 3617, Groupe Hospitalier de la Pitié Salpêtrière, Paris, France.
  • Schara U; Universitätsklinikum, Essen, Germany.
  • Straathof CS; LUMC, Leiden, the Netherlands.
  • D'Angelo MG; IRCCS Eugenio Medea, Lecco, Italy.
  • Bernert G; G.v. Preyer'sches Kinderspital, Wien, Austria.
  • Cuisset JM; CHRU de Lille, Lille, France.
  • Finkel RS; Nemours Children's Hospital, Orlando, Florida.
  • Goemans N; University Hospitals Leuven, Leuven, Belgium.
  • Rummey C; 4Pharma, Liestal, Switzerland.
  • Leinonen M; 4Pharma, Liestal, Switzerland.
  • Mayer OH; Division of Pulmonology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania.
  • Spagnolo P; Santhera Pharmaceuticals, Liestal, Switzerland.
  • Meier T; Santhera Pharmaceuticals, Liestal, Switzerland.
  • McDonald CM; University of California Davis Medical Center, Sacramento, California.
Pediatr Pulmonol ; 52(4): 508-515, 2017 04.
Article em En | MEDLINE | ID: mdl-27571420

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Respiração / Ubiquinona / Distrofia Muscular de Duchenne / Antioxidantes Tipo de estudo: Clinical_trials Limite: Adolescent / Child / Female / Humans / Male Idioma: En Revista: Pediatr Pulmonol Assunto da revista: PEDIATRIA Ano de publicação: 2017 Tipo de documento: Article País de afiliação: Bélgica

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Respiração / Ubiquinona / Distrofia Muscular de Duchenne / Antioxidantes Tipo de estudo: Clinical_trials Limite: Adolescent / Child / Female / Humans / Male Idioma: En Revista: Pediatr Pulmonol Assunto da revista: PEDIATRIA Ano de publicação: 2017 Tipo de documento: Article País de afiliação: Bélgica