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Longitudinal In Vivo Monitoring of the CNS Demonstrates the Efficacy of Gene Therapy in a Sheep Model of CLN5 Batten Disease.
Mitchell, Nadia L; Russell, Katharina N; Wellby, Martin P; Wicky, Hollie E; Schoderboeck, Lucia; Barrell, Graham K; Melzer, Tracy R; Gray, Steven J; Hughes, Stephanie M; Palmer, David N.
Afiliação
  • Mitchell NL; Department of Molecular Biosciences, Faculty of Agriculture and Life Sciences, Lincoln University, Lincoln 7647, New Zealand; Department of Radiology, University of Otago, Christchurch 8140, New Zealand.
  • Russell KN; Department of Molecular Biosciences, Faculty of Agriculture and Life Sciences, Lincoln University, Lincoln 7647, New Zealand.
  • Wellby MP; Department of Molecular Biosciences, Faculty of Agriculture and Life Sciences, Lincoln University, Lincoln 7647, New Zealand.
  • Wicky HE; Department of Biochemistry, Brain Health Research Centre, University of Otago, Dunedin 9054, New Zealand.
  • Schoderboeck L; Department of Biochemistry, Brain Health Research Centre, University of Otago, Dunedin 9054, New Zealand.
  • Barrell GK; Department of Molecular Biosciences, Faculty of Agriculture and Life Sciences, Lincoln University, Lincoln 7647, New Zealand.
  • Melzer TR; Department of Medicine, University of Otago, Christchurch 8140, New Zealand.
  • Gray SJ; Gene Therapy Center and Department of Ophthalmology, University of North Carolina, Chapel Hill, NC 27599, USA.
  • Hughes SM; Department of Biochemistry, Brain Health Research Centre, University of Otago, Dunedin 9054, New Zealand.
  • Palmer DN; Department of Molecular Biosciences, Faculty of Agriculture and Life Sciences, Lincoln University, Lincoln 7647, New Zealand; Department of Radiology, University of Otago, Christchurch 8140, New Zealand. Electronic address: david.palmer@lincoln.ac.nz.
Mol Ther ; 26(10): 2366-2378, 2018 10 03.
Article em En | MEDLINE | ID: mdl-30078766

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Encéfalo / Terapia Genética / Proteínas de Membrana / Lipofuscinoses Ceroides Neuronais Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Animals / Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Nova Zelândia

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Encéfalo / Terapia Genética / Proteínas de Membrana / Lipofuscinoses Ceroides Neuronais Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Animals / Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Nova Zelândia