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A Phase 1b Trial to Assess the Pharmacokinetics of Ezutromid in Pediatric Duchenne Muscular Dystrophy Patients on a Balanced Diet.
Muntoni, Francesco; Tejura, Bina; Spinty, Stefan; Roper, Helen; Hughes, Imelda; Layton, Gary; Davies, Kay E; Harriman, Shawn; Tinsley, Jonathon.
Afiliação
  • Muntoni F; Dubowitz Neuromuscular Centre, University College London Institute of Child Health, London, UK.
  • Tejura B; Summit Therapeutics, Abingdon, UK.
  • Spinty S; Alder Hey Children's NHS Foundation Trust, Liverpool, UK.
  • Roper H; Birmingham Heartlands Hospital, Heart of England NHS Foundation Trust, Birmingham, UK.
  • Hughes I; Royal Manchester Children's Hospital, Central Manchester University Hospitals NHS Foundation Trust, UK.
  • Layton G; ParamStat Limited, Ash, UK.
  • Davies KE; MRC Functional Genomics Unit, University of Oxford, Department of Physiology Anatomy and Genetics, Oxford, UK.
  • Harriman S; Summit Therapeutics, Abingdon, UK.
  • Tinsley J; Summit Therapeutics, Abingdon, UK.
Clin Pharmacol Drug Dev ; 8(7): 922-933, 2019 10.
Article em En | MEDLINE | ID: mdl-30650257

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Benzoxazóis / Distrofia Muscular de Duchenne Tipo de estudo: Clinical_trials Limite: Adolescent / Child / Humans / Male Idioma: En Revista: Clin Pharmacol Drug Dev Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Benzoxazóis / Distrofia Muscular de Duchenne Tipo de estudo: Clinical_trials Limite: Adolescent / Child / Humans / Male Idioma: En Revista: Clin Pharmacol Drug Dev Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Reino Unido