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Utilization of a novel Sendai virus vector in ex vivo gene therapy for hemophilia A.
Yamaki, Yuni; Fukushima, Takashi; Yoshida, Naomi; Nishimura, Ken; Fukuda, Aya; Hisatake, Koji; Aso, Masayuki; Sakasai, Tomoki; Kijima-Tanaka, Junko; Miwa, Yoshihiro; Nakanishi, Mahito; Sumazaki, Ryo; Takada, Hidetoshi.
Afiliação
  • Yamaki Y; Department of Pediatrics, University of Tsukuba Hospital, 2-1-1 Amakubo, Tsukuba, Ibaraki, 305-8576, Japan. yamaki-kgs@umin.ac.jp.
  • Fukushima T; Department of Pediatrics, University of Tsukuba Hospital, 2-1-1 Amakubo, Tsukuba, Ibaraki, 305-8576, Japan.
  • Yoshida N; Department of Child Health, Faculty of Medicine, University of Tsukuba, Ibaraki, Japan.
  • Nishimura K; Department of Pediatric Tumor, Saitama Medical University International Medical Center, Saitama, Japan.
  • Fukuda A; Biotechnology Institute for Drug Discovery, National Institute of Advanced Industrial Science and Technology, Ibaraki, Japan.
  • Hisatake K; TOKIWA-Bio Inc., Ibaraki, Japan.
  • Aso M; Graduate School of Comprehensive Human Sciences, University of Tsukuba, Ibaraki, Japan.
  • Sakasai T; Graduate School of Comprehensive Human Sciences, University of Tsukuba, Ibaraki, Japan.
  • Kijima-Tanaka J; Graduate School of Comprehensive Human Sciences, University of Tsukuba, Ibaraki, Japan.
  • Miwa Y; CellGenTech, Inc., Chiba, Japan.
  • Nakanishi M; Department of Molecular Pharmacology, Faculty of Medicine, University of Tsukuba, Ibaraki, Japan.
  • Sumazaki R; Department of Molecular Pharmacology, Faculty of Medicine, University of Tsukuba, Ibaraki, Japan.
  • Takada H; Department of Molecular Pharmacology, Faculty of Medicine, University of Tsukuba, Ibaraki, Japan.
Int J Hematol ; 113(4): 493-499, 2021 Apr.
Article em En | MEDLINE | ID: mdl-33385293

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Vírus Sendai / Vetores Genéticos / Hemofilia A Tipo de estudo: Prognostic_studies Limite: Animals / Humans Idioma: En Revista: Int J Hematol Assunto da revista: HEMATOLOGIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Japão

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Vírus Sendai / Vetores Genéticos / Hemofilia A Tipo de estudo: Prognostic_studies Limite: Animals / Humans Idioma: En Revista: Int J Hematol Assunto da revista: HEMATOLOGIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Japão